(Q33340517)

English

A pilot study of in vivo liver-directed gene transfer with an adenoviral vector in partial ornithine transcarbamylase deficiency

scientific article

Statements

A pilot study of in vivo liver-directed gene transfer with an adenoviral vector in partial ornithine transcarbamylase deficiency (English)
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Steven E Raper
Marc Yudkoff
Narendra Chirmule
Guang-Ping Gao
Ziv J Haskal
Emma E Furth
Kathleen J Propert
Michael B Robinson
Susan Magosin
Heather Simoes
Lisa Speicher
Joseph Hughes
John Tazelaar
Nelson A Wivel
Mark L Batshaw

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