(Q33444755)
Statements
1 reference
Miglustat in adult and juvenile patients with Niemann-Pick disease type C: long-term data from a clinical trial (English)
1 reference
James E Wraith
1 reference
Darleen Vecchio
1 reference
Elizabeth Jacklin
1 reference
Harbajan Chadha-Boreham
1 reference
Cécile Luzy
1 reference
Ruben Giorgino
1 reference
31 December 2009
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
1 reference
Identifiers
1 reference