(Q33730680)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

title

First-in-human mutation-targeted siRNA phase Ib trial of an inherited skin disorder (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

Kenneth Boucher

6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

13

Leonard M Milstone

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

author name string

Sancy A Leachman

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

Robyn P Hickerson

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

Mary E Schwartz

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

Stephen L Hutcherson

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

C David Hansen

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

Mark J Eliason

8

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

G Susan Srivatsa

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

Douglas J Kornbrust

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

Frances Jd Smith

11

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

Wh Irwin McLean

12

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

Roger L Kaspar

14

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

publication date

24 November 2009

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

volume

18

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

page(s)

442-446

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

issue

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

siRNA silencing of keratinocyte-specific GFP expression in a transgenic mouse skin model.

12 February 2020

cites work

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Knocking down barriers: advances in siRNA delivery

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

The promises and pitfalls of RNA-interference-based therapeutics

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Stability study of unmodified siRNA and relevance to clinical use.

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Therapeutic siRNAs for dominant genetic skin disorders including pachyonychia congenita.

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

The business of RNAi therapeutics

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

RNAi therapeutics: an update on delivery

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Sequence- and target-independent angiogenesis suppression by siRNA via TLR3

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Delivering silence: advancements in developing siRNA therapeutics.

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Single-nucleotide-specific siRNA targeting in a dominant-negative skin model

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Challenges in developing therapies for rare diseases including pachyonychia congenita

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

The genetic basis of pachyonychia congenita.

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Clinical and pathological features of pachyonychia congenita

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Overcoming functional redundancy to elicit pachyonychia congenita-like nail lesions in transgenic mice

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

An inducible mouse model for epidermolysis bullosa simplex: implications for gene therapy

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

Evaluation of the safety, tolerability and pharmacokinetics of ALN-RSV01, a novel RNAi antiviral therapeutic directed against respiratory syncytial virus (RSV).

21 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839285

30 October 2018

Identifiers

DOI

10.1038/MT.2009.273

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19935778%20AND%20SRC:MED&resulttype=core&format=json

12 February 2020

1 reference