(Q34110253)

31 July 2017

title

Meganucleases can restore the reading frame of a mutated dystrophin (English)

1 reference

31 July 2017

P Chapdelaine

1

1 reference

31 July 2017

C Pichavant

2

1 reference

31 July 2017

J Rousseau

3

1 reference

31 July 2017

F Pâques

4

1 reference

31 July 2017

J P Tremblay

5

1 reference

31 July 2017

publication date

15 April 2010

1 reference

31 July 2017

1 reference

31 July 2017

volume

17

1 reference

31 July 2017

issue

7

1 reference

31 July 2017

page(s)

846-858

1 reference

Induction of homologous recombination in mammalian chromosomes by using the I-SceI system of Saccharomyces cerevisiae

31 July 2017

cites work

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

Introduction of double-strand breaks into the genome of mouse cells by expression of a rare-cutting endonuclease

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

Dystrophin: the protein product of the Duchenne muscular dystrophy locus

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Log-PCR: a new tool for immediate and cost-effective diagnosis of up to 85% of dystrophin gene mutations.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Transduction efficiency and immune response associated with the administration of AAV8 vector into dog skeletal muscle

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Synthetic intron improves transduction efficiency of trans-splicing adeno-associated viral vectors.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Sustained AAV-mediated dystrophin expression in a canine model of Duchenne muscular dystrophy with a brief course of immunosuppression

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Microutrophin delivery through rAAV6 increases lifespan and improves muscle function in dystrophic dystrophin/utrophin-deficient mice

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Stem and progenitor cells in skeletal muscle development, maintenance, and therapy

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Muscle-derived stem cells: characterization and potential for cell-mediated therapy

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Autologous transplantation of SM/C-2.6(+) satellite cells transduced with micro-dystrophin CS1 cDNA by lentiviral vector into mdx mice.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Mesoangioblast stem cells ameliorate muscle function in dystrophic dogs

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Dystrophin expression in muscles of duchenne muscular dystrophy patients after high-density injections of normal myogenic cells.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

First test of a "high-density injection" protocol for myogenic cell transplantation throughout large volumes of muscles in a Duchenne muscular dystrophy patient: eighteen months follow-up

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

PTC124 targets genetic disorders caused by nonsense mutations

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

PTC124, nonsense mutations and Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Nanopolymers improve delivery of exon skipping oligonucleotides and concomitant dystrophin expression in skeletal muscle of mdx mice

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Sustained dystrophin expression induced by peptide-conjugated morpholino oligomers in the muscles of mdx mice.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Efficient targeting of a SCID gene by an engineered single-chain homing endonuclease

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Highly efficient endogenous human gene correction using designed zinc-finger nucleases

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Homing endonuclease structure and function

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Meganucleases and DNA double-strand break-induced recombination: perspectives for gene therapy

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

A yeast-endonuclease-generated DNA break induces antigenic switching in Trypanosoma brucei

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Directed evolution and substrate specificity profile of homing endonuclease I-SceI.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Computational redesign of endonuclease DNA binding and cleavage specificity

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Engineering of large numbers of highly specific homing endonucleases that induce recombination on novel DNA targets

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

A combinatorial approach to create artificial homing endonucleases cleaving chosen sequences

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Molecular basis of xeroderma pigmentosum group C DNA recognition by engineered meganucleases

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Engineered I-CreI derivatives cleaving sequences from the human XPC gene can induce highly efficient gene correction in mammalian cells

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Transplantation of myoblasts from a transgenic mouse overexpressing dystrophin produced only a relatively small increase of dystrophin-positive membrane

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Chromosomal translocations induced at specified loci in human stem cells.

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Initiation of DNA fragmentation during apoptosis induces phosphorylation of H2AX histone at serine 139

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Targeted approaches for gene therapy and the emergence of engineered meganucleases

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

A canine minidystrophin is functional and therapeutic in mdx mice

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Protein estimation directly from SDS-PAGE loading buffer for standardization of samples from cell lysates or tissue homogenates before Western blot analysis

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Nucleofection of muscle-derived stem cells and myoblasts with phiC31 integrase: stable expression of a full-length-dystrophin fusion gene by human myoblasts

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.26

7 January 2021

Identifiers

DOI

10.1038/GT.2010.26

1 reference

Dimensions Publication ID

31 July 2017

1023491052

0 references

Fatcat ID

release_o7enqz3dmjgb5iskpcv7nft4tm

1 reference

Fatcat

https://api.fatcat.wiki/v0/release/o7enqz3dmjgb5iskpcv7nft4tm

24 November 2022

mapped directly with Wikidata item

1 reference