(Q34493345)

English

A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency

scientific article

Statements

A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency (English)
Barbara K Burton
Manisha Balwani
François Feillet
T Andrew Burrow
Carmen Camarena Grande
Mahmut Coker
Alejandra Consuelo-Sánchez
Patrick Deegan
Maja Di Rocco
Gregory M Enns
Richard Erbe
Fatih Ezgu
Katryn N Furuya
Christina Laukaitis
Edward G Neilan
Scott Nightingale
Heidi Peters
Maurizio Scarpa
K Otfried Schwab
Vratislav Smolka
Marnie Wood
Zachary Goodman
Yijun Yang
Stephen Eckert
Sandra Rojas-Caro
Anthony G Quinn
1 September 2015
1010-1020

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