(Q34783922)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

title

Long-term safety and efficacy of factor IX gene therapy in hemophilia B (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

0 references

0 references

coagulation factor IX

0 references

0 references

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Marco Della Peruta

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Katherine A. High

20

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

3

Edward G D Tuddenham

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

1

Amit C Nathwani

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

19

Federico Mingozzi

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

author name string

Ulreke M Reiss

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Cecilia Rosales

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Jenny McIntosh

6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Elsa Lheriteau

8

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Nishal Patel

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Deepak Raj

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Anne Riddell

11

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Jun Pie

12

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Savita Rangarajan

13

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

David Bevan

14

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Michael Recht

15

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Yu-Min Shen

16

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Kathleen G Halka

17

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Etiena Basner-Tschakarjan

18

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

James Allay

21

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Mark A Kay

22

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Catherine Y C Ng

23

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Junfang Zhou

24

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Maria Cancio

25

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Christopher L Morton

26

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

John T Gray

27

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Deokumar Srivastava

28

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Arthur W Nienhuis

29

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

Andrew M Davidoff

30

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

language of work or name

English

0 references

publication date

1 November 2014

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

The New England Journal of Medicine

23 February 2020

published in

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

volume

371

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

issue

21

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

page(s)

1994-2004

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

Systemic errors in quantitative polymerase chain reaction titration of self-complementary adeno-associated viral vectors and improved alternative methods

23 February 2020

cites work

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

The hope and reality of long-acting hemophilia products

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Adenovirus-associated virus vector-mediated gene transfer in hemophilia B

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Good manufacturing practice production of self-complementary serotype 8 adeno-associated viral vector for a hemophilia B clinical trial

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Analysis of low frequency bleeding data: the association of joint bleeds according to baseline FVIII activity levels.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Epidemiology of coagulation disorders

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Randomized, multicenter trial comparing tacrolimus plus mycophenolate mofetil to tacrolimus plus steroids in hepatitis C virus-positive recipients of living donor liver transplantation.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Walk a mile in the moccasins of people with haemophilia

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

CD8(+) T-cell responses to adeno-associated virus capsid in humans

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4278802

26 October 2018

Identifiers

DOI

10.1056/NEJMOA1407309

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25409372%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

PubMed publication ID

25409372

1 reference