(Q34883547)

5 August 2017

title

Rescue of splicing-mediated intron loss maximizes expression in lentiviral vectors containing the human ubiquitin C promoter (English)

1 reference

5 August 2017

1

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5 August 2017

4

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5 August 2017

Georgia R Lill

2

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5 August 2017

Eric H Gschweng

series ordinal

3

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5 August 2017

language of work or name

English

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publication date

17 December 2014

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5 August 2017

published in

Nucleic Acids Research

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5 August 2017

volume

43

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5 August 2017

issue

1

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5 August 2017

page(s)

682-690

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Creative Commons Attribution-NonCommercial 4.0 International

5 August 2017

copyright license

start time

8 May 2017

1 reference

April 2022 Public Data File from Crossref

copyright status

copyrighted

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cites work

Preclinical demonstration of lentiviral vector-mediated correction of immunological and metabolic abnormalities in models of adenosine deaminase deficiency

1 reference

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β-globin gene transfer to human bone marrow for sickle cell disease.

8 July 2018

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Integrase-defective lentiviral vectors as a delivery platform for targeted modification of adenosine deaminase locus

8 July 2018

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy

8 July 2018

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Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome.

8 July 2018

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Yin Yang 1 intronic binding sequences and splicing elicit intron-mediated enhancement of ubiquitin C gene expression.

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Splicing kinetics and transcript release from the chromatin compartment limit the rate of Lipid A-induced gene expression

8 July 2018

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

8 July 2018

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Live Cell Monitoring of hiPSC Generation and Differentiation Using Differential Expression of Endogenous microRNAs

8 July 2018

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Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease

8 July 2018

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Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

8 July 2018

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Mechanisms controlling titer and expression of bidirectional lentiviral and gammaretroviral vectors.

8 July 2018

1 reference

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A potent enhancer element in the 5'-UTR intron is crucial for transcriptional regulation of the human ubiquitin C gene.

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients

8 July 2018

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Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

8 July 2018

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Achieving targeted and quantifiable alteration of mRNA splicing with Morpholino oligos

8 July 2018

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Coordinate dual-gene transgenesis by lentiviral vectors carrying synthetic bidirectional promoters.

8 July 2018

1 reference

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Regulation of alternative RNA splicing by exon definition and exon sequences in viral and mammalian gene expression

8 July 2018

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LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1

8 July 2018

1 reference

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Advances in lentiviral vector design for gene-modification of hematopoietic stem cells.

8 July 2018

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RNA 3' readthrough of oncoretrovirus and lentivirus: implications for vector safety and efficacy

8 July 2018

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Germline transmission and tissue-specific expression of transgenes delivered by lentiviral vectors

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Lentiviral vectors for enhanced gene expression in human hematopoietic cells

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Self-inactivating lentivirus vector for safe and efficient in vivo gene delivery

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

A third-generation lentivirus vector with a conditional packaging system

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

The green fluorescent protein

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4288199

Equal potency of gammaretroviral and lentiviral SIN vectors for expression of O6-methylguanine-DNA methyltransferase in hematopoietic cells

8 July 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25520191

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Comparison of various envelope proteins for their ability to pseudotype lentiviral vectors and transduce primitive hematopoietic cells from human blood

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25520191

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1093/NAR/GKU1312

1 reference

5 August 2017

1 reference

5 August 2017

1 reference