(Q34985105)

5 August 2017

title

Induction of immune tolerance to coagulation factor IX antigen by in vivo hepatic gene transfer (English)

1 reference

5 August 2017

1

Federico Mingozzi

1 reference

5 August 2017

8

Katherine A. High

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727926

29 December 2023

author name string

Yi-Lin Liu

2

1 reference

5 August 2017

Eric Dobrzynski

3

1 reference

5 August 2017

Antje Kaufhold

4

1 reference

5 August 2017

Jian Hua Liu

5

1 reference

5 August 2017

YuQin Wang

6

1 reference

5 August 2017

Valder R. Arruda

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727926

29 December 2023

Roland W. Herzog

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727926

29 December 2023

language of work or name

English

0 references

publication date

1 May 2003

1 reference

full work available at URL

5 August 2017

http://www.jci.org/articles/view/16887/files/pdf

file format

Portable Document Format

online access status

open access

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727926

https://europepmc.org/articles/PMC154443

29 December 2023

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727926

https://europepmc.org/articles/PMC154443?pdf=render

29 December 2023

file format

Portable Document Format

online access status

open access

content deliverer

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727926

https://doi.org/10.1172/jci200316887

29 December 2023

online access status

open access

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727926

Journal of Clinical Investigation

29 December 2023

published in

1 reference

5 August 2017

volume

111

1 reference

5 August 2017

issue

9

1 reference

5 August 2017

page(s)

1347-1356

1 reference

Improved hepatic gene transfer by using an adeno-associated virus serotype 5 vector

5 August 2017

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Persistent expression of canine factor IX in hemophilia B canines

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8 July 2018

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8 July 2018

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8 July 2018

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8 July 2018

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Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors

8 July 2018

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Therapeutic levels of functional human factor X in rats after retroviral-mediated hepatic gene therapy.

8 July 2018

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The molecular basis of haemophilia A and B.

8 July 2018

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Antigen-driven bystander suppression after oral administration of antigens

8 July 2018

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Immune tolerance to a defined heterologous antigen after intrasplenic hepatocyte transplantation: implications for gene therapy

8 July 2018

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Influence of vector dose on factor IX-specific T and B cell responses in muscle-directed gene therapy

8 July 2018

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Induction of T-cell tolerance to an MHC class I alloantigen by gene therapy

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Sustained phenotypic correction of hemophilia B dogs with a factor IX null mutation by liver-directed gene therapy

26 October 2018

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A deviant immune response to viral proteins and transgene product is generated on subretinal administration of adenovirus and adeno-associated virus

26 October 2018

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Risk and prevention of anti-factor IX formation in AAV-mediated gene transfer in the context of a large deletion of F9.

26 October 2018

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Muscle-directed gene transfer and transient immune suppression result in sustained partial correction of canine hemophilia B caused by a null mutation

26 October 2018

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Adenovirus-mediated factor VIII gene expression results in attenuated anti-factor VIII-specific immunity in hemophilia A mice compared with factor VIII protein infusion

26 October 2018

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Induction of tolerance to human factor VIII in mice

26 October 2018

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26 October 2018

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Intravenous administration of an E1/E3-deleted adenoviral vector induces tolerance to factor IX in C57BL/6 mice

26 October 2018

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26 October 2018

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26 October 2018

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26 October 2018

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Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors

26 October 2018

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Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

26 October 2018

1 reference

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Adeno-associated viral vector-mediated gene transfer of human blood coagulation factor IX into mouse liver

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=154443

Sustained phenotypic correction of murine hemophilia A by in vivo gene therapy

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=154443

Human factor IX corrects the bleeding diathesis of mice with hemophilia B.

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=154443

Sustained expression of therapeutic levels of human factor VIII in mice

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=154443

Induction of stable prenatal tolerance to beta-galactosidase by in utero gene transfer into preimmune sheep fetuses

26 October 2018

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12 December 2020

Induction and mechanism of action of transforming growth factor-beta-secreting Th3 regulatory cells

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12 December 2020

Gamma delta T lymphocytes regulate the induction and maintenance of oral tolerance

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12 December 2020

Use of a liver-specific promoter reduces immune response to the transgene in adenoviral vectors

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12 December 2020

Identifiers

DOI

10.1172/JCI200316887

1 reference

National Center for Biotechnology Information

5 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=12727926

29 December 2023

1 reference

5 August 2017

1 reference