(Q35153108)

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Correction of dystrophin expression in cells from Duchenne muscular dystrophy patients through genomic excision of exon 51 by zinc finger nucleases

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scholarly article

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Europe PubMed Central

6 August 2017

Correction of dystrophin expression in cells from Duchenne muscular dystrophy patients through genomic excision of exon 51 by zinc finger nucleases (English)

1 reference

Europe PubMed Central

6 August 2017

Duchenne muscular dystrophy

1 reference

based on heuristic

inferred from title

Pablo Perez-Pinera

4

1 reference

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25492562%20AND%20SRC:MED&resulttype=core&format=json

11 June 2020

author name string

David G Ousterout

1

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11 June 2020

Ami M Kabadi

2

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11 June 2020

Pratiksha I Thakore

3

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11 June 2020

Matthew T Brown

5

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11 June 2020

William H Majoros

6

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11 June 2020

Timothy E Reddy

7

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11 June 2020

Charles A Gersbach

8

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11 June 2020

publication date

10 December 2014

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6 August 2017

Molecular Therapy

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11 June 2020

23

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11 June 2020

3

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11 June 2020

523-532

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11 June 2020

Synthetic zinc finger proteins: the advent of targeted gene regulation and genome modification technologies

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Recombinase-mediated reprogramming and dystrophin gene addition in mdx mouse induced pluripotent stem cells.

1 reference

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1 reference

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13 July 2018

An online bioinformatics tool predicts zinc finger and TALE nuclease off-target cleavage

1 reference

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1 reference

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1 reference

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13 July 2018

Gene correction of a duchenne muscular dystrophy mutation by meganuclease-enhanced exon knock-in.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Reading frame correction by targeted genome editing restores dystrophin expression in cells from Duchenne muscular dystrophy patients.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering

1 reference

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13 July 2018

An ex vivo gene therapy approach to treat muscular dystrophy using inducible pluripotent stem cells

1 reference

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Targeted Gene Addition of Microdystrophin in Mice Skeletal Muscle via Human Myoblast Transplantation

1 reference

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A TALEN genome-editing system for generating human stem cell-based disease models

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Highly active zinc-finger nucleases by extended modular assembly

1 reference

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13 July 2018

TALENs: a widely applicable technology for targeted genome editing

1 reference

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13 July 2018

Human ES- and iPS-derived myogenic progenitors restore DYSTROPHIN and improve contractility upon transplantation in dystrophic mice.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Gene targeting to the ROSA26 locus directed by engineered zinc finger nucleases

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Immortalized pathological human myoblasts: towards a universal tool for the study of neuromuscular disorders

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Targeted gene correction of α1-antitrypsin deficiency in induced pluripotent stem cells

1 reference

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13 July 2018

Endonucleases: tools to correct the dystrophin gene.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

In situ genetic correction of the sickle cell anemia mutation in human induced pluripotent stem cells using engineered zinc finger nucleases

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Therapeutic applications of the ΦC31 integrase system

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13 July 2018

Site-specific gene correction of a point mutation in human iPS cells derived from an adult patient with sickle cell disease

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Revealing off-target cleavage specificities of zinc-finger nucleases by in vitro selection

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

An unbiased genome-wide analysis of zinc-finger nuclease specificity

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

In vivo genome editing restores haemostasis in a mouse model of haemophilia

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Selection-free zinc-finger-nuclease engineering by context-dependent assembly (CoDA)

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Enhancing zinc-finger-nuclease activity with improved obligate heterodimeric architectures

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

The status of exon skipping as a therapeutic approach to duchenne muscular dystrophy

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Genome editing with engineered zinc finger nucleases

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Autonomous zinc-finger nuclease pairs for targeted chromosomal deletion.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

A rapid and general assay for monitoring endogenous gene modification

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Quantification of zinc finger nuclease-associated toxicity

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

The generation of zinc finger proteins by modular assembly.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

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1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Directed evolution of an enhanced and highly efficient FokI cleavage domain for zinc finger nucleases

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

ZiFiT (Zinc Finger Targeter): an updated zinc finger engineering tool

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

13 July 2018

Modular system for the construction of zinc-finger libraries and proteins

1 reference

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1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

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1 reference

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1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

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1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4351462

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1 reference

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1 reference

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1 reference

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1 reference

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1 reference

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1 reference

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1 reference

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1 reference

https://pubmed.ncbi.nlm.nih.gov/25492562

12 December 2020

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10.1038/MT.2014.234

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11 June 2020

release_arrcshp7rrhozeteo7y3ux6vum

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24 November 2022

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mapped directly with Wikidata item

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Europe PubMed Central

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11 June 2020

1 reference

Europe PubMed Central

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11 June 2020

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