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Gene therapy for mucopolysaccharidosis.
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scholarly article
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
review article
1 reference
stated in
Europe PubMed Central
title
Gene therapy for mucopolysaccharidosis
(English)
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
main subject
gene therapy
0 references
author
Assumpció Bosch
series ordinal
1
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
author name string
Jean Michel Heard
series ordinal
2
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
publication date
1 January 2003
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
published in
International Review of Neurobiology
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
volume
55
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
page(s)
271-296
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
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A deviant immune response to viral proteins and transgene product is generated on subretinal administration of adenovirus and adeno-associated virus
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Correction of mucopolysaccharidosis type I fibroblasts by retroviral-mediated transfer of the human alpha-L-iduronidase gene
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Neuroprotective gene therapy for Huntington's disease using a polymer encapsulated BHK cell line engineered to secrete human CNTF.
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7 January 2021
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7 January 2021
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Behavioral consequences of bone marrow transplantation in the treatment of murine mucopolysaccharidosis type VII.
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7 January 2021
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7 January 2021
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Correction of murine mucopolysaccharidosis type VII (MPS VII) by bone marrow transplantation and gene transfer therapy
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency
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Crossref
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7 January 2021
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Long-term and significant correction of brain lesions in adult mucopolysaccharidosis type VII mice using recombinant AAV vectors.
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer.
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Functional correction of established central nervous system deficits in an animal model of lysosomal storage disease with feline immunodeficiency virus-based vectors
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7 January 2021
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Immune response to enzyme replacement therapy: clinical signs of hypersensitivity reactions and altered enzyme distribution in a high titre rat model.
1 reference
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Lentiviral vector transduction of hematopoietic stem cells that mediate long-term reconstitution of lethally irradiated mice
1 reference
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Murine mucopolysaccharidosis type I: targeted disruption of the murine alpha-L-iduronidase gene
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Recombinant adeno-associated virus type 2, 4, and 5 vectors: transduction of variant cell types and regions in the mammalian central nervous system.
1 reference
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Enzyme replacement therapy by fibroblast transplantation in a case of Hunter syndrome
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
based on heuristic
inferred from DOI database lookup
Central nervous system delivery of recombinant ciliary neurotrophic factor by polymer encapsulated differentiated C2C12 myoblasts
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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inferred from DOI database lookup
Production and neurotropism of lentivirus vectors pseudotyped with lyssavirus envelope glycoproteins.
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
based on heuristic
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Caprine mucopolysaccharidosis IIID: a preliminary trial of enzyme replacement therapy.
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
based on heuristic
inferred from DOI database lookup
Elimination of lysosomal storage in brains of MPS VII mice treated by intrathecal administration of an adeno-associated virus vector
1 reference
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Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Safety and efficacy of recombinant human alpha-galactosidase A replacement therapy in Fabry's disease
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Crossref
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7 January 2021
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Targeted disruption of the arylsulfatase B gene results in mice resembling the phenotype of mucopolysaccharidosis VI
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
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Long-term in vitro correction of alpha-L-iduronidase deficiency (Hurler syndrome) in human bone marrow.
1 reference
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Crossref
reference URL
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7 January 2021
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Sulfamidase deficiency in a family of Dachshunds: a canine model of mucopolysaccharidosis IIIA (Sanfilippo A).
1 reference
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Crossref
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7 January 2021
based on heuristic
inferred from DOI database lookup
Hurler and Hunter syndromes: mutual correction of the defect in cultured fibroblasts
1 reference
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Crossref
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https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
based on heuristic
inferred from DOI database lookup
Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.
1 reference
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Crossref
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7 January 2021
based on heuristic
inferred from DOI database lookup
Molecular basis of feline beta-glucuronidase deficiency: an animal model of mucopolysaccharidosis VII.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
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7 January 2021
based on heuristic
inferred from DOI database lookup
Extensive beta-glucuronidase activity in murine central nervous system after adenovirus-mediated gene transfer to brain
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Enzyme therapy for Gaucher disease: the first 5 years
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Correction of lysosomal enzyme deficiency in various organs of beta-glucuronidase-deficient mice by allogeneic bone marrow transplantation
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Allogeneic bone marrow transplantation for lysosomal storage diseases. The European Group for Bone Marrow Transplantation
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Viral-mediated gene transfer to mouse primary neural progenitor cells.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Mucopolysaccharidosis in a Cat with Arylsulfatase B Deficiency: A Model of Maroteaux-Lamy Syndrome
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Long-term and high-dose trials of enzyme replacement therapy in the canine model of mucopolysaccharidosis I.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Enzyme-replacement therapy in mucopolysaccharidosis I.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Enzyme replacement therapy in feline mucopolysaccharidosis I.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Adenovirus-mediated gene therapy for corneal clouding in mice with mucopolysaccharidosis type VII.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Phosphohexosyl components of a lysosomal enzyme are recognized by pinocytosis receptors on human fibroblasts
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Engraftment of genetically engineered amniotic epithelial cells corrects lysosomal storage in multiple areas of the brain in mucopolysaccharidosis type VII mice
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Multi-organ, multi-lineage engraftment by a single bone marrow-derived stem cell
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
The future for treatment by bone marrow transplantation for adrenoleukodystrophy, metachromatic leukodystrophy, globoid cell leukodystrophy and Hurler syndrome
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Mouse model of Sanfilippo syndrome type B produced by targeted disruption of the gene encoding alpha-N-acetylglucosaminidase
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Phenotype correction in retinal pigment epithelium in murine mucopolysaccharidosis VII by adenovirus-mediated gene transfer
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Neuronal activity-dependent membrane traffic at the neuromuscular junction.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Correction of lysosomal storage in the liver and spleen of MPS VII mice by implantation of genetically modified skin fibroblasts
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Continuous systemic secretion of a lysosomal enzyme by genetically modified mouse skin fibroblasts.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Long-term delivery of a lysosomal enzyme by genetically modified fibroblasts in dogs
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Enzyme replacement therapy for murine mucopolysaccharidosis type VII leads to improvements in behavior and auditory function
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Neurotropism and retrograde axonal transport of a canine adenoviral vector: a tool for targeting key structures undergoing neurodegenerative processes.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Restoration of arylsulphatase B activity in human mucopolysaccharidosis-type-VI fibroblasts by retroviral-vector-mediated gene transfer
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Targeting of proteins to the lysosome.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Bone marrow transplantation has a significant effect on enzyme levels and storage of glycosaminoglycans in tissues and in isolated hepatocytes of mucopolysaccharidosis type VII mice
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Synthetic glycopeptide substrates for receptor-mediated endocytosis by macrophages
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Delivery of recombinant gene products to the central nervous system with nonautologous cells in alginate microcapsules
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Treatment of a lysosomal storage disease, mucopolysaccharidosis VII, with microencapsulated recombinant cells
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Somatic gene therapy for a neurodegenerative disease using microencapsulated recombinant cells
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
In vivo delivery of human alpha-L-iduronidase in mice implanted with neo-organs
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Recognition and receptor-mediated uptake of a lysosomal enzyme, alpha-l-iduronidase, by cultured human fibroblasts
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Enzyme replacement therapy for murine mucopolysaccharidosis type VII
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Infusion of alpha-galactosidase A reduces tissue globotriaosylceramide storage in patients with Fabry disease
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
In vivo protein transduction: delivery of a biologically active protein into the mouse
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Primary adult human astrocytes as an ex vivo vehicle for beta-glucuronidase delivery in the brain
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Enzyme replacement in a canine model of Hurler syndrome
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Sustained production of beta-glucuronidase from localized sites after AAV vector gene transfer results in widespread distribution of enzyme and reversal of lysosomal storage lesions in a large volume of brain in mucopolysaccharidosis VII mice.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Correction of enzyme deficiency in mice by allogeneic bone marrow transplantation with total lymphoid irradiation
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Active site mutant transgene confers tolerance to human beta-glucuronidase without affecting the phenotype of MPS VII mice.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Neural progenitor cell engraftment corrects lysosomal storage throughout the MPS VII mouse brain
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Nonablative neonatal marrow transplantation attenuates functional and physical defects of beta-glucuronidase deficiency.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
A canine model of human alpha-L-iduronidase deficiency
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using nonprimate lentiviral vectors.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
N-acetylglucosamine 6-sulphatase deficiency in a Nubian goat: a model of Sanfilippo syndrome type D (mucopolysaccharidosis IIID)
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Recombinant human alpha-glucosidase from rabbit milk in Pompe patients.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Enzyme replacement with recombinant beta-glucuronidase in murine mucopolysaccharidosis type VII: impact of therapy during the first six weeks of life on subsequent lysosomal storage, growth, and survival
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Enzyme replacement in murine mucopolysaccharidosis type VII: neuronal and glial response to beta-glucuronidase requires early initiation of enzyme replacement therapy
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Treatment of lysosomal storage disease in MPS VII mice using a recombinant adeno-associated virus
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Long-term outcome of Hurler syndrome following bone marrow transplantation
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Clinical and morphologic features of mucopolysaccharidosis type II in a dog: naturally occurring model of Hunter syndrome
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Restoration of normal lysosomal function in mucopolysaccharidosis type VII cells by retroviral vector-mediated gene transfer
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Gene transfer of low levels of beta-glucuronidase corrects hepatic lysosomal storage in a large animal model of mucopolysaccharidosis VII.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
The HIV Tat protein transduction domain improves the biodistribution of beta-glucuronidase expressed from recombinant viral vectors.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Transduction of hepatocytes after neonatal delivery of a Moloney murine leukemia virus based retroviral vector results in long-term expression of beta-glucuronidase in mucopolysaccharidosis VII dogs
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Arylsulfatase B-deficient mucopolysaccharidosis in rats
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Short-term enzyme replacement in the murine model of Sanfilippo syndrome type B.
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Significantly increased expression of beta-glucuronidase in the central nervous system of mucopolysaccharidosis type VII mice from the latency-associated transcript promoter in a nonpathogenic herpes simplex virus type 1 vector
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Phenotype correction in murine mucopolysaccharidosis type VII by transplantation of human amniotic epithelial cells after adenovirus-mediated gene transfer
1 reference
stated in
Crossref
reference URL
https://api.crossref.org/works/10.1016%2FS0074-7742%2803%2901012-2
retrieved
7 January 2021
based on heuristic
inferred from DOI database lookup
Identifiers
DOI
10.1016/S0074-7742(03)01012-2
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
PubMed publication ID
12968541
1 reference
stated in
Europe PubMed Central
PubMed publication ID
12968541
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12968541%20AND%20SRC:MED&resulttype=core&format=json
retrieved
7 November 2019
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