(Q35667391)

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Treatment of phenylketonuria using minicircle-based naked-DNA gene transfer to murine liver

scientific article published on 29 July 2014

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scholarly article

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Europe PubMed Central

PubMed publication ID

9 August 2017

Treatment of phenylketonuria using minicircle-based naked-DNA gene transfer to murine liver (English)

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Europe PubMed Central

PubMed publication ID

9 August 2017

phenylketonuria

1 reference

based on heuristic

inferred from title

Thierry VandenDriessche

6

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Europe PubMed Central

PMC publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

author name string

Hiu Man Viecelli

1

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8 June 2020

Richard P Harbottle

2

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8 June 2020

Suet Ping Wong

3

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

Andrea Schlegel

4

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

Marinee K Chuah

5

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8 June 2020

Cary O Harding

7

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8 June 2020

Beat Thöny

8

1 reference

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

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publication date

29 July 2014

1 reference

Europe PubMed Central

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9 August 2017

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Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

60

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Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

3

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

1035-1043

1 reference

Europe PubMed Central

PMC publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

Computationally designed liver-specific transcriptional modules and hyperactive factor IX improve hepatic gene therapy

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Minicircle DNA vectors achieve sustained expression reflected by active chromatin and transcriptional level

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

The extragenic spacer length between the 5' and 3' ends of the transgene expression cassette affects transgene silencing from plasmid-based vectors

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Quantification of phenylalanine hydroxylase activity by isotope-dilution liquid chromatography-electrospray ionization tandem mass spectrometry.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

The AAV vector toolkit: poised at the clinical crossroads

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Minicircle DNA electrotransfer for efficient tissue-targeted gene delivery.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

State-of-the-art gene-based therapies: the road ahead

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Development of S/MAR minicircles for enhanced and persistent transgene expression in the mouse liver

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

A robust system for production of minicircle DNA vectors

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Minicircle DNA-based gene therapy coupled with immune modulation permits long-term expression of α-L-iduronidase in mice with mucopolysaccharidosis type I

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Translating Sleeping Beauty transposition into cellular therapies: victories and challenges

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Conserved role of intragenic DNA methylation in regulating alternative promoters

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Comparison of adeno-associated virus pseudotype 1, 2, and 8 vectors administered by intramuscular injection in the treatment of murine phenylketonuria

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Image-guided, lobe-specific hydrodynamic gene delivery to swine liver

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Progress and prospects: the design and production of plasmid vectors.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Persistent episomal transgene expression in liver following delivery of a scaffold/matrix attachment region containing non-viral vector.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Episomal vectors for gene therapy

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

CpG-free plasmids confer reduced inflammation and sustained pulmonary gene expression.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Correction of murine PKU following AAV-mediated intramuscular expression of a complete phenylalanine hydroxylating system

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Minimally invasive and selective hydrodynamic gene therapy of liver segments in the pig and human

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Gender differences in serotype 2 adeno-associated virus biodistribution after administration to rodent salivary glands

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Innate immune response induced by gene delivery vectors

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Complete correction of hyperphenylalaninemia following liver-directed, recombinant AAV2/8 vector-mediated gene therapy in murine phenylketonuria.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Low therapeutic threshold for hepatocyte replacement in murine phenylketonuria.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

On the biological significance of DNA methylation

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Long-term enzymatic and phenotypic correction in the phenylketonuria mouse model by adeno-associated virus vector-mediated gene transfer

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Dwarfism and low insulin-like growth factor-1 due to dopamine depletion in Pts-/- mice rescued by feeding neurotransmitter precursors and H4-biopterin

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

High levels of foreign gene expression in hepatocytes after tail vein injections of naked plasmid DNA.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

A new DNA vehicle for nonviral gene delivery: supercoiled minicircle

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Mouse models of human phenylketonuria

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

12 July 2018

Administration-route and gender-independent long-term therapeutic correction of phenylketonuria (PKU) in a mouse model by recombinant adeno-associated virus 8 pseudotyped vector-mediated gene transfer

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Complete restoration of phenylalanine oxidation in phenylketonuria mouse by a self-complementary adeno-associated virus vector

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Long-term correction of hyperphenylalaninemia by AAV-mediated gene transfer leads to behavioral recovery in phenylketonuria mice

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

AAV vector integration sites in mouse hepatocellular carcinoma.

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

An araC-controlled bacterial cre expression system to produce DNA minicircle vectors for nuclear and mitochondrial gene therapy.

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Minicircle-DNA production by site specific recombination and protein-DNA interaction chromatography.

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Hydrodynamics-based transfection in animals by systemic administration of plasmid DNA.

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Hydrodynamic liver gene transfer mechanism involves transient sinusoidal blood stasis and massive hepatocyte endocytic vesicles.

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Silencing of episomal transgene expression in liver by plasmid bacterial backbone DNA is independent of CpG methylation

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Expression of a transgene encoded on a non-viral episomal vector is not subject to epigenetic silencing by cytosine methylation

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Muscle damage after delivery of naked plasmid DNA into skeletal muscles is batch dependent.

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Direct comparison of hepatocyte-specific expression cassettes following adenoviral and nonviral hydrodynamic gene transfer

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Minicircle DNA vectors devoid of bacterial DNA result in persistent and high-level transgene expression in vivo

1 reference

https://api.crossref.org/works/10.1002%2FHEP.27104

21 January 2018

Structural impact of hydrodynamic injection on mouse liver

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4449723

25 September 2018

Phenylketonuria

1 reference

https://pubmed.ncbi.nlm.nih.gov/24585515

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Transgene loss and changes in the promoter methylation status as determinants for expression duration in nonviral gene transfer for factor IX

1 reference

https://pubmed.ncbi.nlm.nih.gov/24585515

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Identifiers

10.1002/HEP.27104

1 reference

Europe PubMed Central

PMC publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

release_ok5i3zlqczhyvlk4gsw426ls2y

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https://api.fatcat.wiki/v0/release/ok5i3zlqczhyvlk4gsw426ls2y

24 November 2022

based on heuristic

mapped directly with Wikidata item

PMC publication ID

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Europe PubMed Central

PMC publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

PubMed publication ID

1 reference

Europe PubMed Central

PMC publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24585515%20AND%20SRC:MED&resulttype=core&format=json

8 June 2020

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