(Q36777548)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

title

Targeted gene addition in human CD34(+) hematopoietic cells for correction of X-linked chronic granulomatous disease (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

X-linked chronic granulomatous disease

10 March 2020

main subject

0 references

author

Kol A Zarember

19

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

Philip D Gregory

21

1 reference

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10 March 2020

Harry Malech

23

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

1

Suk See De Ravin

1 reference

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10 March 2020

9

Uimook Choi

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

17

Colin Sweeney

1 reference

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10 March 2020

8

Narda Theobald

1 reference

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10 March 2020

16

Sherry Koontz

1 reference

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10 March 2020

20

Madhusudan V Peshwa

1 reference

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10 March 2020

22

Fyodor D Urnov

1 reference

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10 March 2020

13

David E Paschon

1 reference

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10 March 2020

2

Andreas Reik

1 reference

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10 March 2020

18

David A Shivak

1 reference

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10 March 2020

3

Pei-Qi Liu

1 reference

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10 March 2020

author name string

Linhong Li

4

1 reference

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10 March 2020

Xiaolin Wu

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

Ling Su

6

1 reference

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10 March 2020

Castle Raley

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

Alexander H Song

10

1 reference

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10 March 2020

Andy Chan

11

1 reference

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10 March 2020

Jocelynn R Pearl

12

1 reference

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10 March 2020

Janet Lee

14

1 reference

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10 March 2020

Hannah Newcombe

15

1 reference

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10 March 2020

publication date

7 March 2016

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

number of pages

6

1 reference

based on heuristic

inferred from page(s)

published in

Nature Biotechnology

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

volume

34

1 reference

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10 March 2020

issue

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

page(s)

424-429

1 reference

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https://scigraph.springernature.com/pub.10.1038/nbt.3513

10 March 2020

exact match

0 references

cites work

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29 September 2017

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29 September 2017

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High-efficiency transduction of primary human hematopoietic stem cells and erythroid lineage-restricted expression by optimized AAV6 serotype vectors in vitro and in a murine xenograft model in vivo

29 September 2017

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Ubiquitous high-level gene expression in hematopoietic lineages provides effective lentiviral gene therapy of murine Wiskott-Aldrich syndrome

29 September 2017

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29 September 2017

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An unbiased genome-wide analysis of zinc-finger nuclease specificity

29 September 2017

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Residual NADPH oxidase and survival in chronic granulomatous disease

29 September 2017

1 reference

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Efficacy of gene therapy for X-linked severe combined immunodeficiency

29 September 2017

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Functional genomics, proteomics, and regulatory DNA analysis in isogenic settings using zinc finger nuclease-driven transgenesis into a safe harbor locus in the human genome

29 September 2017

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Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease

29 September 2017

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Targeted gene addition into a specified location in the human genome using designed zinc finger nucleases

29 September 2017

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Highly efficient endogenous human gene correction using designed zinc-finger nucleases

29 September 2017

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29 September 2017

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29 September 2017

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Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease

29 September 2017

1 reference

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29 September 2017

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29 September 2017

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Genome engineering with TALENs and ZFNs: repair pathways and donor design

27 June 2018

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27 June 2018

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A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency

27 June 2018

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Homology-driven genome editing in hematopoietic stem and progenitor cells using ZFN mRNA and AAV6 donors.

5 September 2018

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Crossref

https://api.crossref.org/works/10.1038%2FNBT.3513

Concentrated RD114-pseudotyped MFGS-gp91phox vector achieves high levels of functional correction of the chronic granulomatous disease oxidase defect in NOD/SCID/beta -microglobulin-/- repopulating mobilized human peripheral blood CD34+ cells

21 January 2018

1 reference

Crossref

https://api.crossref.org/works/10.1038%2FNBT.3513

21 January 2018

Identifiers

DOI

10.1038/NBT.3513

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26950749%20AND%20SRC:MED&resulttype=core&format=json

10 March 2020

PubMed publication ID

26950749

1 reference