(Q38287263)

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Immune responses to intramuscular administration of alipogene tiparvovec (AAV1-LPL(S447X)) in a phase II clinical trial of lipoprotein lipase deficiency gene therapy

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scholarly article

1 reference

Europe PubMed Central

1 September 2017

Immune responses to intramuscular administration of alipogene tiparvovec (AAV1-LPL(S447X)) in a phase II clinical trial of lipoprotein lipase deficiency gene therapy (English)

1 reference

Europe PubMed Central

1 September 2017

phase II clinical trial

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inferred from title

Eleonora Aronica

4

object named as

Eleonora Aronica

1 reference

Europe PubMed Central

1 September 2017

author name string

Valerie Ferreira

1

1 reference

Europe PubMed Central

1 September 2017

Jaap Twisk

2

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Europe PubMed Central

1 September 2017

Karin Kwikkers

3

1 reference

Europe PubMed Central

1 September 2017

Diane Brisson

5

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Europe PubMed Central

1 September 2017

Julie Methot

6

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Europe PubMed Central

1 September 2017

Harald Petry

7

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Europe PubMed Central

1 September 2017

Daniel Gaudet

8

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Europe PubMed Central

1 September 2017

publication date

28 February 2014

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Europe PubMed Central

1 September 2017

Human Gene Therapy

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Europe PubMed Central

1 September 2017

25

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Europe PubMed Central

1 September 2017

3

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Europe PubMed Central

1 September 2017

180-188

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Europe PubMed Central

1 September 2017

Human Treg responses allow sustained recombinant adeno-associated virus-mediated transgene expression

1 reference

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Immune responses to AAV vectors: overcoming barriers to successful gene therapy

1 reference

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Efficacy and long-term safety of alipogene tiparvovec (AAV1-LPLS447X) gene therapy for lipoprotein lipase deficiency: an open-label trial

1 reference

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1 reference

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Phase 2 clinical trial of a recombinant adeno-associated viral vector expressing α1-antitrypsin: interim results

1 reference

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The complex and evolving story of T cell activation to AAV vector-encoded transgene products

1 reference

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Sustained transgene expression despite T lymphocyte responses in a clinical trial of rAAV1-AAT gene therapy

1 reference

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1 reference

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Modulation of tolerance to the transgene product in a nonhuman primate model of AAV-mediated gene transfer to liver.

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Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

1 reference

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Regional intravascular delivery of AAV-2-F.IX to skeletal muscle achieves long-term correction of hemophilia B in a large animal model

1 reference

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AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B.

1 reference

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Skeletal muscle fibers express major histocompatibility complex class II antigens independently of inflammatory infiltrates in inflammatory myopathies

1 reference

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Human lipoprotein lipase: relationship of activity, heparin affinity, and conformation as studied with monoclonal antibodies

1 reference

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Increased intracellular triglyceride in C(2)C(12) muscle cells transfected with human lipoprotein lipase

1 reference

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The role of the Fas lytic pathway in a perforin-less CTL hybridoma.

1 reference

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Preexisting immunity and low expression in primates highlight translational challenges for liver-directed AAV8-mediated gene therapy

1 reference

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Effects of transient immunosuppression on adenoassociated, virus-mediated, liver-directed gene transfer in rhesus macaques and implications for human gene therapy

1 reference

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Limb-girdle muscular dystrophy type 2D gene therapy restores alpha-sarcoglycan and associated proteins

1 reference

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Lack of toxicity of alpha-sarcoglycan overexpression supports clinical gene transfer trial in LGMD2D.

1 reference

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Phase I trial of intramuscular injection of a recombinant adeno-associated virus serotype 2 alphal-antitrypsin (AAT) vector in AAT-deficient adults

1 reference

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Gene therapy for lipoprotein lipase deficiency: working toward clinical application

1 reference

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1 reference

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Effect of alipogene tiparvovec (AAV1-LPL(S447X)) on postprandial chylomicron metabolism in lipoprotein lipase-deficient patients

1 reference

https://pubmed.ncbi.nlm.nih.gov/24299335

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Increased expression of HLA ABC class I antigens by muscle fibres in Duchenne muscular dystrophy, inflammatory myopathy, and other neuromuscular disorders

1 reference

https://pubmed.ncbi.nlm.nih.gov/24299335

12 December 2020

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inferred from PubMed ID database lookup

Immunohistological alterations in muscle of patients with amyotrophic lateral sclerosis: mononuclear cell phenotypes and expression of MHC products

1 reference

https://pubmed.ncbi.nlm.nih.gov/24299335

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Identifiers

10.1089/HUM.2013.169

1 reference

Europe PubMed Central

1 September 2017

1 reference

Europe PubMed Central

1 September 2017

1 reference

Europe PubMed Central

1 September 2017

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