(Q39287288)
Statements
European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: a 10-year experience (English)
M E Kruijshaar
A Toscano
P Laforêt
C Angelini
M Roberts
K Rösler
P A van Doorn
P Y K Van den Bergh
J Vissing
B Schoser
European Pompe Consortium
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