(Q40027548)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:18180772%20AND%20SRC:MED&resulttype=core&format=json

31 December 2019

title

Self-inactivating gammaretroviral vectors for gene therapy of X-linked severe combined immunodeficiency (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:18180772%20AND%20SRC:MED&resulttype=core&format=json

severe combined immunodeficiency

31 December 2019

main subject

gene therapy

0 references

1 reference

8

1 reference

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31 December 2019

Adrian Thrasher

12

1 reference

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31 December 2019

author name string

Susannah I Thornhill

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:18180772%20AND%20SRC:MED&resulttype=core&format=json

31 December 2019

Steven J Howe

3

1 reference

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31 December 2019

Meera Ulaganathan

4

1 reference

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31 December 2019

Elke Grassman

5

1 reference

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31 December 2019

David Williams

6

1 reference

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31 December 2019

Bernhard Schiedlmeier

7

1 reference

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31 December 2019

H Bobby Gaspar

9

1 reference

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31 December 2019

Christine Kinnon

10

1 reference

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31 December 2019

Christopher Baum

11

1 reference

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31 December 2019

Axel Schambach

2

1 reference

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31 December 2019

publication date

8 January 2008

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31 December 2019

1 reference

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31 December 2019

volume

16

1 reference

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31 December 2019

issue

3

1 reference

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31 December 2019

page(s)

590-598

1 reference

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Hematopoietic stem-cell transplantation for the treatment of severe combined immunodeficiency.

31 December 2019

cites work

1 reference

12 December 2020

Design of 5' untranslated sequences in retroviral vectors developed for medical use.

1 reference

12 December 2020

Restoration of lymphoid populations in a murine model of X-linked severe combined immunodeficiency by a gene-therapy approach

1 reference

12 December 2020

Intrinsic defects of B cell function in X-linked severe combined immunodeficiency

1 reference

12 December 2020

Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease

1 reference

12 December 2020

Plat-E: an efficient and stable system for transient packaging of retroviruses

1 reference

12 December 2020

High-level transgene expression in human hematopoietic progenitors and differentiated blood lineages after transduction with improved lentiviral vectors

1 reference

12 December 2020

Context Dependence of Different Modules for Posttranscriptional Enhancement of Gene Expression from Retroviral Vectors

1 reference

12 December 2020

Lentivirus-mediated gene transfer in primary T cells is enhanced by a central DNA flap.

1 reference

12 December 2020

Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy

1 reference

12 December 2020

High-level transduction and gene expression in hematopoietic repopulating cells using a human immunodeficiency [correction of imunodeficiency] virus type 1-based lentiviral vector containing an internal spleen focus forming virus promoter

1 reference

12 December 2020

Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning

1 reference

12 December 2020

Induction of T cell development from hematopoietic progenitor cells by delta-like-1 in vitro.

1 reference

12 December 2020

Gene therapy of X-linked severe combined immunodeficiency

1 reference

12 December 2020

A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency

1 reference

12 December 2020

Long-term survival and transplantation of haemopoietic stem cells for immunodeficiencies: report of the European experience 1968–99

1 reference

12 December 2020

LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1

1 reference

12 December 2020

Molecular defects in human severe combined immunodeficiency and approaches to immune reconstitution

1 reference

12 December 2020

Self-inactivating retroviral vectors with improved RNA processing.

1 reference

12 December 2020

Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector

1 reference

12 December 2020

Severe combined immunodeficiency. A model disease for molecular immunology and therapy

1 reference

12 December 2020

Equal potency of gammaretroviral and lentiviral SIN vectors for expression of O6-methylguanine-DNA methyltransferase in hematopoietic cells

1 reference

12 December 2020

Woodchuck hepatitis virus post-transcriptional regulatory element deleted from X protein and promoter sequences enhances retroviral vector titer and expression

1 reference

12 December 2020

Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.

1 reference

12 December 2020

Overcoming promoter competition in packaging cells improves production of self-inactivating retroviral vectors

1 reference

12 December 2020

Cell-culture assays reveal the importance of retroviral vector design for insertional genotoxicity

1 reference

12 December 2020

Lentiviral vectors containing an enhancer-less ubiquitously acting chromatin opening element (UCOE) provide highly reproducible and stable transgene expression in hematopoietic cells

1 reference

12 December 2020

Vector integration is nonrandom and clustered and influences the fate of lymphopoiesis in SCID-X1 gene therapy

1 reference

12 December 2020

Gammaretrovirus-mediated correction of SCID-X1 is associated with skewed vector integration site distribution in vivo

1 reference

12 December 2020

Generation and analysis of interleukin-4 deficient mice

1 reference

12 December 2020

Novel retroviral vectors for efficient expression of the multidrug resistance (mdr-1) gene in early hematopoietic cells.

1 reference

12 December 2020

Involvement of the c-kit receptor in the adhesion of hematopoietic stem cells to stromal cells

1 reference

12 December 2020

Defective lymphoid development in mice lacking expression of the common cytokine receptor gamma chain.

1 reference

12 December 2020

Lymphoid development in mice with a targeted deletion of the interleukin 2 receptor gamma chain.

1 reference

12 December 2020

High-frequency cell surface expression of a foreign protein in murine hematopoietic stem cells using a new retroviral vector.

1 reference

12 December 2020

Atypical X-Linked Severe Combined Immunodeficiency Due to Possible Spontaneous Reversion of the Genetic Defect in T Cells

1 reference

12 December 2020

Long-term immune reconstitution and outcome after HLA-nonidentical T-cell-depleted bone marrow transplantation for severe combined immunodeficiency: a European retrospective study of 116 patients.

1 reference

12 December 2020

Enhanced human cell engraftment in mice deficient in RAG2 and the common cytokine receptor gamma chain

1 reference

12 December 2020

Functional role of interleukin-4 (IL-4) and IL-7 in the development of X-linked severe combined immunodeficiency

1 reference

12 December 2020

Identifiers

DOI

10.1038/SJ.MT.6300393

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:18180772%20AND%20SRC:MED&resulttype=core&format=json

31 December 2019

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:18180772%20AND%20SRC:MED&resulttype=core&format=json

31 December 2019

1 reference