(Q40181522)

18 September 2017

title

Design of tissue-specific regulatory cassettes for high-level rAAV-mediated expression in skeletal and cardiac muscle (English)

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18 September 2017

2

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author name string

Maja Z Salva

1

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18 September 2017

Phillip Wl Tai

3

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18 September 2017

Eiko Nishiuchi

4

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18 September 2017

Paul Gregorevic

5

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18 September 2017

James M Allen

6

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18 September 2017

Eric E Finn

7

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18 September 2017

Quynh G Nguyen

8

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18 September 2017

Michael J Blankinship

9

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18 September 2017

Leonard Meuse

10

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18 September 2017

Jeffrey S Chamberlain

11

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18 September 2017

Stephen D Hauschka

12

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18 September 2017

publication date

1 February 2007

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18 September 2017

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18 September 2017

volume

15

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18 September 2017

issue

2

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18 September 2017

page(s)

320-329

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Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

18 September 2017

cites work

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Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart

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Sustained whole-body functional rescue in congestive heart failure and muscular dystrophy hamsters by systemic gene transfer

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Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein

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Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector

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Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

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Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors

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Efficient transduction of skeletal muscle using vectors based on adeno-associated virus serotype 6.

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7 January 2021

Correction of glycogen storage disease type II by an adeno-associated virus vector containing a muscle-specific promoter

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7 January 2021

Robust systemic transduction with AAV9 vectors in mice: efficient global cardiac gene transfer superior to that of AAV8.

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Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo

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7 January 2021

Analysis of muscle creatine kinase regulatory elements in recombinant adenoviral vectors

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7 January 2021

Muscle-specific promoters may be necessary for adeno-associated virus-mediated gene transfer in the treatment of muscular dystrophies.

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7 January 2021

Adeno-associated virus vector-mediated gene transfer into dystrophin-deficient skeletal muscles evokes enhanced immune response against the transgene product

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7 January 2021

CTLA4Ig delivered by high-capacity adenoviral vector induces stable expression of dystrophin in mdx mouse muscle

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7 January 2021

AAV vector-mediated microdystrophin expression in a relatively small percentage of mdx myofibers improved the mdx phenotype

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7 January 2021

Myosin regulatory elements as vectors for gene transfer by intramuscular injection

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7 January 2021

Synthetic muscle promoters: activities exceeding naturally occurring regulatory sequences

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7 January 2021

Immune evasion by muscle-specific gene expression in dystrophic muscle

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7 January 2021

Therapeutic levels of factor IX expression using a muscle-specific promoter and adeno-associated virus serotype 1 vector

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7 January 2021

Femoral intra-arterial injection: a tool to deliver and assess recombinant AAV constructs in rodents whole hind limb

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7 January 2021

Muscle creatine kinase sequence elements regulating skeletal and cardiac muscle expression in transgenic mice

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7 January 2021

Analysis of muscle creatine kinase gene regulatory elements in skeletal and cardiac muscles of transgenic mice

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7 January 2021

E-box sites and a proximal regulatory region of the muscle creatine kinase gene differentially regulate expression in diverse skeletal muscles and cardiac muscle of transgenic mice

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7 January 2021

Differences in the function of three conserved E-boxes of the muscle creatine kinase gene in cultured myocytes and in transgenic mouse skeletal and cardiac muscle

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7 January 2021

Transgenic and tissue culture analyses of the muscle creatine kinase enhancer Trex control element in skeletal and cardiac muscle indicate differences in gene expression between muscle types

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7 January 2021

Multiple regulatory elements contribute differentially to muscle creatine kinase enhancer activity in skeletal and cardiac muscle

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7 January 2021

Viral vectors for gene transfer of micro-, mini-, or full-length dystrophin

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7 January 2021

Multiple roles for the MyoD basic region in transmission of transcriptional activation signals and interaction with MEF2

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7 January 2021

Mechanism of synergy between TATA and initiator: synergistic binding of TFIID following a putative TFIIA-induced isomerization

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7 January 2021

Characterization of multiple enhancer regions upstream of the apolipoprotein(a) gene

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7 January 2021

Alpha-myosin heavy chain gene regulation: delineation and characterization of the cardiac muscle-specific enhancer and muscle-specific promoter

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7 January 2021

Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy

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7 January 2021

Mutation of the IIB myosin heavy chain gene results in muscle fiber loss and compensatory hypertrophy.

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7 January 2021

Improved cardiac gene transfer by transcriptional and transductional targeting of adeno-associated viral vectors.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300027

7 January 2021

Effect of muscle origin and phenotype on satellite cell muscle-specific gene expression

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300027

7 January 2021

Expression of dystrophin driven by the 1.35-kb MCK promoter ameliorates muscular dystrophy in fast, but not in slow muscles of transgenic mdx mice

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300027

7 January 2021

Differing patterns of capillary distribution in fish and mammalian skeletal muscle

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7 January 2021

Improved adeno-associated virus vector production with transfection of a single helper adenovirus gene, E4orf6.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300027

7 January 2021

rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300027

7 January 2021

Force-velocity relations and myosin heavy chain isoform compositions of skinned fibres from rat skeletal muscle

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7 January 2021

Three myosin heavy chain isoforms in type 2 skeletal muscle fibres.

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https://api.crossref.org/works/10.1038%2FSJ.MT.6300027

7 January 2021

Forced expression of dystrophin deletion constructs reveals structure-function correlations.

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7 January 2021

Identifiers

DOI

10.1038/SJ.MT.6300027

1 reference

18 September 2017

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