(Q41889977)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

title

A preclinical approach for gene therapy of beta-thalassemia (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

0 references

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

Stefano Rivella

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

Laura Breda

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

8

Patricia J Giardina

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

3

Carla Casu

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

5

Luca Cartegni

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

2

Dorothy A Kleinert

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

6

Eitan Fibach

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

author name string

Laura Casula

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

Irene Mancini

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

language of work or name

English

0 references

publication date

1 August 2010

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

number of pages

7

1 reference

Annals of the New York Academy of Sciences

inferred from page(s)

published in

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

volume

1202

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

page(s)

134-140

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

Gene therapy in thalassemia and hemoglobinopathies.

10 February 2020

cites work

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Future alternative therapies for β-thalassemia

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Gene therapy. Beta-thalassemia treatment succeeds, with a caveat

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

A phase I/II clinical trial of beta-globin gene therapy for beta-thalassemia

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Therapeutic globin gene delivery using lentiviral vectors.

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

The cHS4 insulator increases the probability of retroviral expression at random chromosomal integration sites.

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Woodchuck hepatitis virus posttranscriptional regulatory element enhances expression of transgenes delivered by retroviral vectors.

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Self-inactivating lentivirus vector for safe and efficient in vivo gene delivery

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

A third-generation lentivirus vector with a conditional packaging system

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Development of a self-inactivating lentivirus vector.

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

A mouse model for beta 0-thalassemia

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Mouse model of human beta zero thalassemia: targeted deletion of the mouse beta maj- and beta min-globin genes in embryonic stem cells

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Base substitution in an intervening sequence of a beta+-thalassemic human globin gene

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Contribution of NF-kappa B and Sp1 binding motifs to the replicative capacity of human immunodeficiency virus type 1: distinct patterns of viral growth are determined by T-cell types

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Linker-scanning mutational analysis of the transcriptional activity of the human immunodeficiency virus type 1 long terminal repeat

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Specific NF-kappa B subunits act in concert with Tat to stimulate human immunodeficiency virus type 1 transcription

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

A novel murine model of Cooley anemia and its rescue by lentiviral-mediated human beta-globin gene transfer

5 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

The two-step liquid culture: a novel procedure for studying maturation of human normal and pathological erythroid precursors

18 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3068625

Nonsense mutations in the human beta-globin gene lead to unexpected levels of cytoplasmic mRNA accumulation

18 August 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/20712784

12 December 2020

inferred from PubMed ID database lookup

Unstable β-globin mRNA in mRNA-deficient β0 thalassemia

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/20712784

12 December 2020

inferred from PubMed ID database lookup

Successful treatment of murine beta-thalassemia intermedia by transfer of the human beta-globin gene

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/20712784

12 December 2020

inferred from PubMed ID database lookup

Identifiers

DOI

10.1111/J.1749-6632.2010.05594.X

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20712784%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

PubMed publication ID

20712784

1 reference