(Q42235082)

19 October 2017

title

Efficient gene delivery to the cone-enriched pig retina by dual AAV vectors (English)

1 reference

19 October 2017

9

1 reference

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7 June 2020

Pasqualina Colella

1

1 reference

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7 June 2020

Ivana Trapani

2

1 reference

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7 June 2020

Maria Laura Bacci

11

1 reference

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7 June 2020

Alberto Auricchio

12

1 reference

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7 June 2020

author name string

G Cesi

3

1 reference

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7 June 2020

A Sommella

4

1 reference

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7 June 2020

A Manfredi

5

1 reference

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7 June 2020

A Puppo

6

1 reference

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7 June 2020

C Iodice

7

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7 June 2020

S Rossi

8

1 reference

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7 June 2020

M Giunti

10

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7 June 2020

publication date

27 February 2014

1 reference

19 October 2017

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24572793%20AND%20SRC:MED&resulttype=core&format=json

7 June 2020

volume

21

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7 June 2020

issue

4

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7 June 2020

page(s)

450-456

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24572793%20AND%20SRC:MED&resulttype=core&format=json

Prevalence of mutations causing retinitis pigmentosa and other inherited retinopathies

7 June 2020

cites work

1 reference

The molecular basis of human retinal and vitreoretinal diseases

21 January 2018

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Effect of gene therapy on visual function in Leber's congenital amaurosis

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Vision 1 year after gene therapy for Leber's congenital amaurosis

21 January 2018

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Safety and efficacy of gene transfer for Leber's congenital amaurosis

21 January 2018

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Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial

21 January 2018

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Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration

21 January 2018

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Three-year follow-up after unilateral subretinal delivery of adeno-associated virus in patients with Leber congenital Amaurosis type 2

21 January 2018

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Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors

21 January 2018

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AAV-mediated photoreceptor transduction of the pig cone-enriched retina

21 January 2018

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Dosage thresholds for AAV2 and AAV8 photoreceptor gene therapy in monkey

21 January 2018

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Fighting blindness with adeno-associated virus serotype 8.

21 January 2018

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Assessment of ocular transduction using single-stranded and self-complementary recombinant adeno-associated virus serotype 2/8.

21 January 2018

1 reference

The human rhodopsin kinase promoter in an AAV5 vector confers rod- and cone-specific expression in the primate retina.

21 January 2018

1 reference

AAV9 targets cone photoreceptors in the nonhuman primate retina

21 January 2018

1 reference

The packaging capacity of adeno-associated virus (AAV) and the potential for wild-type-plus AAV gene therapy vectors

21 January 2018

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Characterization of genome integrity for oversized recombinant AAV vector

21 January 2018

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Evidence for the failure of adeno-associated virus serotype 5 to package a viral genome > or = 8.2 kb.

21 January 2018

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Effect of genome size on AAV vector packaging

21 January 2018

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An update on the genetics of usher syndrome

21 January 2018

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Expression in cochlea and retina of myosin VIIa, the gene product defective in Usher syndrome type 1B

21 January 2018

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Myosin VIIa, the product of the Usher 1B syndrome gene, is concentrated in the connecting cilia of photoreceptor cells.

21 January 2018

1 reference

Function of MYO7A in the human RPE and the validity of shaker1 mice as a model for Usher syndrome 1B

21 January 2018

1 reference

Localization of Usher 1 proteins to the photoreceptor calyceal processes, which are absent from mice

21 January 2018

1 reference

Packaging capacity of adeno-associated virus serotypes: impact of larger genomes on infectivity and postentry steps

21 January 2018

1 reference

Self-complementary recombinant adeno-associated viral vectors: packaging capacity and the role of rep proteins in vector purity.

21 January 2018

1 reference

Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice.

21 January 2018

1 reference

Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant

21 January 2018

1 reference

Trans-splicing vectors expand the utility of adeno-associated virus for gene therapy

21 January 2018

1 reference

Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison

21 January 2018

1 reference

Expanding adeno-associated viral vector capacity: a tale of two vectors.

21 January 2018

1 reference

A hybrid vector system expands adeno-associated viral vector packaging capacity in a transgene-independent manner

21 January 2018

1 reference

Oversized AAV transductifon is mediated via a DNA-PKcs-independent, Rad51C-dependent repair pathway

21 January 2018

1 reference

Proteasome inhibitors enhance gene delivery by AAV virus vectors expressing large genomes in hemophilia mouse and dog models: a strategy for broad clinical application

21 January 2018

1 reference

Homologous recombination mediates functional recovery of dysferlin deficiency following AAV5 gene transfer

21 January 2018

1 reference

Retinal gene therapy with a large MYO7A cDNA using adeno-associated virus

21 January 2018

1 reference

Limitations of encapsidation of recombinant self-complementary adeno-associated viral genomes in different serotype capsids and their quantitation

21 January 2018

1 reference

Myosin7a deficiency results in reduced retinal activity which is improved by gene therapy

21 January 2018

1 reference

Efficient trans-splicing in the retina expands the utility of adeno-associated virus as a vector for gene therapy.

21 January 2018

1 reference

Effects of adeno-associated virus DNA hairpin structure on recombination

21 January 2018

1 reference

Host cell DNA repair pathways in adeno-associated viral genome processing

21 January 2018

1 reference

Distribution and density of medium- and short-wavelength selective cones in the domestic pig retina

21 January 2018

1 reference

MicroRNA-restricted transgene expression in the retina

21 January 2018

1 reference

Combined rod and cone transduction by adeno-associated virus 2/8.

21 January 2018

1 reference

Evaluation of Italian patients with leber congenital amaurosis due to AIPL1 mutations highlights the potential applicability of gene therapy

21 January 2018

1 reference

Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retina

21 January 2018

1 reference

Long-term retinal function and structure rescue using capsid mutant AAV8 vector in the rd10 mouse, a model of recessive retinitis pigmentosa.

21 January 2018

1 reference

Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors

21 January 2018

1 reference

AAV2/8 vectors purified from culture medium with a simple and rapid protocol transduce murine liver, muscle, and retina efficiently

21 January 2018

1 reference

High throughput production, screening and analysis of adeno-associated viral vectors

21 January 2018

1 reference

Case 15-2009: a man with coma after cardiac arrest

21 January 2018

1 reference

inferred from DOI database lookup

7 January 2021

based on heuristic

Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue

1 reference

inferred from DOI database lookup

7 January 2021

based on heuristic

Effective delivery of large genes to the retina by dual AAV vectors

1 reference