(Q36797248)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

title

Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Olivier Christophe

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

John H. McVey

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Simon N. Waddington

11

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Katherine A. High

17

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

8

Edward G D Tuddenham

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

23

Amit C Nathwani

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

15

Federico Mingozzi

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

author name string

Jenny McIntosh

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Cecilia Rosales

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Doyoung Lee

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Samira Rabbanian

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Deepak Raj

6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Nishil Patel

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Arthur W Nienhuis

12

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

John T Gray

13

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Paolo Fagone

14

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Shang-Zhen Zhou

16

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Maria Cancio

18

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Catherine Y C Ng

19

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Junfang Zhou

20

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Christopher L Morton

21

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

Andrew M Davidoff

22

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

language of work or name

English

0 references

publication date

20 February 2013

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

volume

121

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

issue

17

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

page(s)

3335-3344

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

describes a project that uses

24 February 2020

ImageQuant

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC3637010/fullTextXML

based on heuristic

inferred from PubMed Central ID database lookup

cites work

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1 reference

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29 September 2017

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AAV-mediated gene transfer in the perinatal period results in expression of FVII at levels that protect against fatal spontaneous hemorrhage.

29 September 2017

1 reference

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Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins.

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3637010

Evidence for the failure of adeno-associated virus serotype 5 to package a viral genome > or = 8.2 kb.

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3637010

Characterization of genome integrity for oversized recombinant AAV vector

29 September 2017

1 reference

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Effect of genome size on AAV vector packaging

29 September 2017

1 reference

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Enhanced factor VIII heavy chain for gene therapy of hemophilia A

29 September 2017

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Antioxidants reduce endoplasmic reticulum stress and improve protein secretion

29 September 2017

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Complete correction of hemophilia A with adeno-associated viral vectors containing a full-size expression cassette

29 September 2017

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Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice.

29 September 2017

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Analysis of factor VIII mediated suppression of lentiviral vector titres

29 September 2017

1 reference

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The enhancing effects of the light chain on heavy chain secretion in split delivery of factor VIII gene

29 September 2017

1 reference

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Efficacy, safety and tolerability of recombinant factor VIII (REFACTO) in patients with haemophilia A: interim data from a postmarketing surveillance study in Germany and Austria

29 September 2017

1 reference

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Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates

29 September 2017

1 reference

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Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver

29 September 2017

1 reference

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Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models

29 September 2017

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29 September 2017

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Bioengineering of coagulation factor VIII for improved secretion

29 September 2017

1 reference

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Phase 1 trial of FVIII gene transfer for severe hemophilia A using a retroviral construct administered by peripheral intravenous infusion

29 September 2017

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29 September 2017

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Structural and functional characteristics of the B-domain-deleted recombinant factor VIII protein, r-VIII SQ.

29 September 2017

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29 September 2017

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29 September 2017

1 reference

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29 September 2017

1 reference

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29 September 2017

1 reference

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A large region (approximately equal to 95 kDa) of human factor VIII is dispensable for in vitro procoagulant activity

29 September 2017

1 reference

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29 September 2017

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5 September 2018

1 reference

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5 September 2018

1 reference

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5 September 2018

1 reference

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5 September 2018

1 reference

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Efficacy and inhibitor development in previously treated patients with haemophilia A switched to a B domain-deleted recombinant factor VIII.

5 September 2018

1 reference

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5 September 2018

1 reference

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The safety and efficacy of B-domain deleted recombinant factor VIII concentrate in patients with severe haemophilia A.

5 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3637010

Expression of human factor VIII by splicing between dimerized AAV vectors

5 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3637010

Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A.

5 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3637010

Assay of factor VIII antigen (VIII:CAg) in 294 haemophilia A patients by a new commercial ELISA using monoclonal antibodies.

5 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3637010

Biochemical, immunological, and in vivo functional characterization of B-domain-deleted factor VIII.

5 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3637010

Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A.

5 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3637010

Definition of an efficient synthetic poly(A) site

5 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/23426947

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Molecular characterization of human B domain-specific anti-factor VIII monoclonal antibodies generated in transgenic mice

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/23426947

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1182/BLOOD-2012-10-462200

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json

24 February 2020

PubMed publication ID

23426947

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23426947%20AND%20SRC:MED&resulttype=core&format=json