(Q42266598)
Statements
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Safety and liver transduction efficacy of rAAV5-cohPBGD in nonhuman primates: a potential therapy for acute intermittent porphyria (English)
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Christof von Kalle
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Manfred Schmidt
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Alberto Benito
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Astrid Pañeda
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Esperanza Lopez-Franco
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Christine Kaeppel
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Carmen Unzu
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Ana Gloria Gil-Royo
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Delia D'Avola
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Stuart G Beattie
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Cristina Olagüe
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Roberto Ferrero
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Ana Sampedro
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Itsaso Mauleon
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Stephan Hermening
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Florence Salmon
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Juan Jose Gavira
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María Eugenia Cornet
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María del Mar Municio
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Harald Petry
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Jesus Prieto
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Antonio Fontanellas
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Gloria González-Aseguinolaza
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1 December 2013
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24
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12
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1007-1017
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Identifiers
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