(Q42413344)

30 October 2017

RNA interference-mediated suppression and replacement of human rhodopsin in vivo (English)

1 reference

30 October 2017

1 reference

Marius Ader

5

0 references

Alberto Auricchio

object named as

Alberto Auricchio

8

1 reference

ORCID Public Data File 2021

author name string

Mary O'Reilly

1

1 reference

30 October 2017

Arpad Palfi

2

1 reference

30 October 2017

Naomi Chadderton

3

1 reference

30 October 2017

Sophia Millington-Ward

4

1 reference

30 October 2017

Thérèse Cronin

6

1 reference

30 October 2017

Thérèse Tuohy

7

1 reference

30 October 2017

Markus Hildinger

9

1 reference

30 October 2017

Amanda Tivnan

10

1 reference

30 October 2017

Niamh McNally

11

1 reference

30 October 2017

Marian M Humphries

12

1 reference

30 October 2017

Anna-Sophia Kiang

13

1 reference

30 October 2017

Pete Humphries

14

1 reference

30 October 2017

Paul F Kenna

15

1 reference

30 October 2017

G Jane Farrar

16

1 reference

30 October 2017

language of work or name

English

0 references

publication date

23 May 2007

1 reference

American Journal of Human Genetics

30 October 2017

1 reference

30 October 2017

81

1 reference

30 October 2017

127-135

1 reference

30 October 2017

1

1 reference

AAV-mediated gene transfer for retinal diseases

30 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Preservation of photoreceptor morphology and function in P23H rats using an allele independent ribozyme.

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Transfection of mammalian cells using linear polyethylenimine is a simple and effective means of producing recombinant adeno-associated virus vectors

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Adeno-associated virus-vectored gene therapy for retinal disease

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

RNA interference improves motor and neuropathological abnormalities in a Huntington's disease mouse model

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Recombinant AAV-mediated gene transfer to the retina: gene therapy perspectives

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Gene therapy for Leber congenital amaurosis

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Electroporation and RNA interference in the rodent retina in vivo and in vitro

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Coupling of RNAi-mediated target downregulation with gene replacement

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

A system for stable expression of short interfering RNAs in mammalian cells

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

On the genetics of retinitis pigmentosa and on mutation-independent approaches to therapeutic intervention

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Hybrid vectors based on adeno-associated virus serotypes 2 and 5 for muscle-directed gene transfer

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Duplexes of 21-nucleotide RNAs mediate RNA interference in cultured mammalian cells

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Isolation of highly infectious and pure adeno-associated virus type 2 vectors with a single-step gravity-flow column.

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Ribozyme uses in retinal gene therapy.

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Gapped BLAST and PSI-BLAST: a new generation of protein database search programs

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Transgenic mice with a rhodopsin mutation (Pro23His): a mouse model of autosomal dominant retinitis pigmentosa

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Long-term doxycycline-regulated transgene expression in the retina of nonhuman primates following subretinal injection of recombinant AAV vectors

28 May 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

RNAi-based suppression and replacement of rds-peripherin in retinal organotypic culture

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Toward a gene therapy for dominant disease: validation of an RNA interference-based mutation-independent approach

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Towards mutation-independent silencing of genes involved in retinal degeneration by RNA interference

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

An RNAi strategy for treatment of amyotrophic lateral sclerosis caused by mutant Cu,Zn superoxide dismutase.

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

RNAi of COL1A1 in mesenchymal progenitor cells.

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

RNAi suppresses polyglutamine-induced neurodegeneration in a model of spinocerebellar ataxia.

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Fast and reliable titration of recombinant adeno-associated virus type-2 using quantitative real-time PCR.

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Structural and functional rescue of murine rod photoreceptors by human rhodopsin transgene.

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa.

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Preferential silencing of a common dominant rhodopsin mutation does not inhibit retinal degeneration in a transgenic model

16 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1950918

Retinopathy induced in mice by targeted disruption of the rhodopsin gene

1 December 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/17564969

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Strategems in vitro for gene therapies directed to dominant mutations

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/17564969

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1086/519025

1 reference

30 October 2017

1 reference

30 October 2017

1 reference