(Q43221778)

16 November 2017

AAV-mediated knockdown of peripherin-2 in vivo using miRNA-based hairpins (English)

1 reference

16 November 2017

3

1 reference

16 November 2017

A Georgiadis

1

1 reference

16 November 2017

M Tschernutter

2

1 reference

16 November 2017

S J Robbie

4

1 reference

16 November 2017

J McIntosh

5

1 reference

16 November 2017

A C Nathwani

6

1 reference

16 November 2017

A J Smith

7

1 reference

16 November 2017

R R Ali

8

1 reference

16 November 2017

10 December 2009

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16 November 2017

1 reference

16 November 2017

17

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16 November 2017

4

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16 November 2017

486-493

1 reference

https://scigraph.springernature.com/pub.10.1038/gt.2009.162

16 November 2017

0 references

cites work

Molecular genetics and prospects for therapy of the inherited retinal dystrophies

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Perspective on genes and mutations causing retinitis pigmentosa

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

On the genetics of retinitis pigmentosa and on mutation-independent approaches to therapeutic intervention

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Prospects for retinal gene replacement therapy.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

The retinal degeneration slow (rds) gene product is a photoreceptor disc membrane-associated glycoprotein.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

The spectrum of retinal dystrophies caused by mutations in the peripherin/RDS gene

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Prevalence of mutations causing retinitis pigmentosa and other inherited retinopathies

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Prevalence of disease-causing mutations in families with autosomal dominant retinitis pigmentosa: a screen of known genes in 200 families

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Effect of gene therapy on visual function in Leber's congenital amaurosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Safety and efficacy of gene transfer for Leber's congenital amaurosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Assessing adenoviral hammerhead ribozyme and small hairpin RNA cassettes in neurons: inhibition of endogenous caspase-3 activity and protection from apoptotic cell death.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Preservation of photoreceptor morphology and function in P23H rats using an allele independent ribozyme.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Ribozyme rescue of photoreceptor cells in P23H transgenic rats: long-term survival and late-stage therapy.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Suppression of mouse rhodopsin expression in vivo by AAV mediated siRNA delivery

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

RNA interference-mediated suppression and replacement of human rhodopsin in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

A transgenic mouse model for gene therapy of rhodopsin-linked Retinitis Pigmentosa

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

RNAi-based suppression and replacement of rds-peripherin in retinal organotypic culture

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Therapeutic benefit derived from RNAi-mediated ablation of IMPDH1 transcripts in a murine model of autosomal dominant retinitis pigmentosa (RP10).

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Improved retinal function in a mouse model of dominant retinitis pigmentosa following AAV-delivered gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Fatality in mice due to oversaturation of cellular microRNA/short hairpin RNA pathways

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Expression profiling reveals off-target gene regulation by RNAi

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

MicroRNA precursors in motion: exportin-5 mediates their nuclear export

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Artificial miRNAs mitigate shRNA-mediated toxicity in the brain: implications for the therapeutic development of RNAi

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

An efficient method to enhance gene silencing by using precursor microRNA designed small hairpin RNAs

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Artificial microRNAs as siRNA shuttles: improved safety as compared to shRNAs in vitro and in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Towards mutation-independent silencing of genes involved in retinal degeneration by RNA interference

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Enhanced gene silencing of HIV-1 specific siRNA using microRNA designed hairpins

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Rapid and stable knockdown of an endogenous gene in retinal pigment epithelium

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

RNAi suppresses polyglutamine-induced neurodegeneration in a model of spinocerebellar ataxia.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Assessment of ocular transduction using single-stranded and self-complementary recombinant adeno-associated virus serotype 2/8.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Gene transfer into the mouse retina mediated by an adeno-associated viral vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Long-term preservation of retinal function in the RCS rat model of retinitis pigmentosa following lentivirus-mediated gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Preferential silencing of a common dominant rhodopsin mutation does not inhibit retinal degeneration in a transgenic model

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

Molecular genetics of macular degeneration

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2009.162

inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

DOI

10.1038/GT.2009.162

1 reference

Dimensions Publication ID

16 November 2017

1004432217

0 references

Fatcat ID

release_m24w6z66grhvnbxnhiurlhxyvq

1 reference

Fatcat

https://api.fatcat.wiki/v0/release/m24w6z66grhvnbxnhiurlhxyvq

mapped directly with Wikidata item

24 November 2022

based on heuristic

1 reference