(Q43283385)
Statements
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Antisense oligonucleotide treatment for a pseudoexon-generating mutation in the NPC1 gene causing Niemann-Pick type C disease (English)
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Daniel Grinberg
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Laura Rodríguez-Pascau
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Maria Josep Coll
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Lluïsa Vilageliu
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1 November 2009
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30
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11
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E993-E1001
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Identifiers
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1 reference