(Q44264343)

1 December 2017

Effective exon skipping and restoration of dystrophin expression by peptide nucleic acid antisense oligonucleotides in mdx mice (English)

1 reference

1 December 2017

1 reference

3

Matthew Wood

1 reference

1 December 2017

Haifang Yin

1

1 reference

PubMed ID

17968354

1 December 2017

Qilong Lu

series ordinal

2

1 reference

PubMed ID

17968354

1 December 2017

language of work or name

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30 October 2007

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1 December 2017

1 reference

1 December 2017

16

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1 December 2017

1

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1 December 2017

38-45

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Subcellular fractionation of dystrophin to the triads of skeletal muscle

1 December 2017

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Specific removal of the nonsense mutation from the mdx dystrophin mRNA using antisense oligonucleotides.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Improved antisense oligonucleotide induced exon skipping in the mdx mouse model of muscular dystrophy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Antisense oligonucleotides: promise and reality.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Comparative analysis of antisense oligonucleotide analogs for targeted DMD exon 46 skipping in muscle cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Antisense properties of peptide nucleic acid

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Tat-mediated delivery of heterologous proteins into cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

In vivo protein transduction: delivery of a biologically active protein into the mouse

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Elucidation of muscle-binding peptides by phage display screening

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Induction of splice correction by cell-penetrating peptide nucleic acids

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Induction of dystrophin expression by exon skipping in mdx mice following intramuscular injection of antisense oligonucleotides complexed with PEG-PEI copolymers

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

RNA targeting with peptide conjugates of oligonucleotides, siRNA and PNA.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Vectorization of morpholino oligomers by the (R-Ahx-R)4 peptide allows efficient splicing correction in the absence of endosomolytic agents.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Cell-penetrating peptide conjugates of peptide nucleic acids (PNA) as inhibitors of HIV-1 Tat-dependent trans-activation in cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Peptide-based delivery of nucleic acids: design, mechanism of uptake and applications to splice-correcting oligonucleotides

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300329

7 January 2021

Identifiers

DOI

10.1038/SJ.MT.6300329

1 reference

1 December 2017

1 reference

PubMed ID

17968354