(Q44405190)

2 December 2017

title

Efficacy and safety of adeno-associated viral vectors based on serotype 8 and 9 vs. lentiviral vectors for hemophilia B gene therapy (English)

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2 December 2017

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Vandendriessche T

1

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2 December 2017

Thorrez L

2

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2 December 2017

Acosta-Sanchez A

3

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2 December 2017

Petrus I

4

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2 December 2017

Wang L

5

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2 December 2017

Ma L

6

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2 December 2017

DE Waele L

7

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2 December 2017

Iwasaki Y

8

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2 December 2017

Gillijns V

9

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2 December 2017

Wilson JM

10

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2 December 2017

Collen D

11

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2 December 2017

Chuah MK

12

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2 December 2017

publication date

26 September 2006

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Journal of Thrombosis and Haemostasis

2 December 2017

published in

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2 December 2017

volume

5

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2 December 2017

issue

1

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2 December 2017

page(s)

16-24

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Lentiviral vectors containing the human immunodeficiency virus type-1 central polypurine tract can efficiently transduce nondividing hepatocytes and antigen-presenting cells in vivo

2 December 2017

cites work

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https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Extrachromosomal recombinant adeno-associated virus vector genomes are primarily responsible for stable liver transduction in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Human immunoglobulin inhibits liver transduction by AAV vectors at low AAV2 neutralizing titers in SCID mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

A limited number of transducible hepatocytes restricts a wide-range linear vector dose response in recombinant adeno-associated virus-mediated liver transduction

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Clades of Adeno-associated viruses are widely disseminated in human tissues.

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Inclusion of the hepatic locus control region, an intron, and untranslated region increases and stabilizes hepatic factor IX gene expression in vivo but not in vitro

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Efficient selection for high-expression transfectants with a novel eukaryotic vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Gene transfer by lentiviral vectors is limited by nuclear translocation and rescued by HIV-1 pol sequences

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

A factor IX-deficient mouse model for hemophilia B gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Lack of germline transmission of vector sequences following systemic administration of recombinant AAV-2 vector in males

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Unrestricted hepatocyte transduction with adeno-associated virus serotype 8 vectors in mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Long-term efficacy of adeno-associated virus serotypes 8 and 9 in hemophilia a dogs and mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Induction of immune tolerance to coagulation factor IX antigen by in vivo hepatic gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Prevention of cytotoxic T lymphocyte responses to factor IX-expressing hepatocytes by gene transfer-induced regulatory T cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Heparin binding directs activation of T cells against adeno-associated virus serotype 2 capsid

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Rapid uncoating of vector genomes is the key to efficient liver transduction with pseudotyped adeno-associated virus vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Targeting ischemic cardiac dysfunction through gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1.

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Biology of AAV serotype vectors in liver-directed gene transfer to nonhuman primates.

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

Multiyear therapeutic benefit of AAV serotypes 2, 6, and 8 delivering factor VIII to hemophilia A mice and dogs

21 January 2018

1 reference

https://api.crossref.org/works/10.1111%2FJ.1538-7836.2006.02220.X

10.1111/J.1538-7836.2006.02220.X

21 January 2018

Identifiers

DOI

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2 December 2017

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