(Q44478509)
Statements
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Limited transgene immune response and long-term expression of human alpha-L-iduronidase in young adult mice with mucopolysaccharidosis type I by liver-directed gene therapy (English)
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L Naldini
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C Di Domenico
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D Di Napoli
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E Gonzalez Y Reyero
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P Di Natale
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1 November 2006
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17
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11
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1112-1121
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Identifiers
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