(Q45007187)

8 December 2017

title

Targeted exon skipping in transgenic hDMD mice: A model for direct preclinical screening of human-specific antisense oligonucleotides (English)

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8 December 2017

Mattie Bremmer-Bout

1

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8 December 2017

Annemieke Aartsma-Rus

2

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8 December 2017

Emile J de Meijer

3

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8 December 2017

Wendy E Kaman

4

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8 December 2017

Anneke A M Janson

5

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8 December 2017

Rolf H A M Vossen

6

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8 December 2017

Gert-Jan B van Ommen

7

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8 December 2017

Johan T den Dunnen

8

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8 December 2017

Judith C T van Deutekom

9

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8 December 2017

publication date

1 August 2004

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8 December 2017

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8 December 2017

volume

10

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8 December 2017

issue

2

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8 December 2017

page(s)

232-240

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Dystrophin: the protein product of the Duchenne muscular dystrophy locus

8 December 2017

cites work

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Characterization of dystrophin in muscle-biopsy specimens from patients with Duchenne's or Becker's muscular dystrophy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

An explanation for the phenotypic differences between patients bearing partial deletions of the DMD locus

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Giant dystrophin deletion associated with congenital cataract and mild muscular dystrophy.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Characterization of translational frame exception patients in Duchenne/Becker muscular dystrophy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Antisense-induced multiexon skipping for Duchenne muscular dystrophy makes more sense

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Chimeric snRNA molecules carrying antisense sequences against the splice junctions of exon 51 of the dystrophin pre-mRNA induce exon skipping and restoration of a dystrophin synthesis in Delta 48-50 DMD cells

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Improved antisense oligonucleotide induced exon skipping in the mdx mouse model of muscular dystrophy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Oligonucleotides against a splicing enhancer sequence led to dystrophin production in muscle cells from a Duchenne muscular dystrophy patient

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Specific removal of the nonsense mutation from the mdx dystrophin mRNA using antisense oligonucleotides.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Target selection for antisense oligonucleotide induced exon skipping in the dystrophin gene.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Enhanced in vivo delivery of antisense oligonucleotides to restore dystrophin expression in adult mdx mouse muscle

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Hyaluronidase enhances recombinant adeno-associated virus (rAAV)-mediated gene transfer in the rat skeletal muscle.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Systemically delivered antisense oligomers upregulate gene expression in mouse tissues

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

An error in dystrophin mRNA processing in golden retriever muscular dystrophy, an animal homologue of Duchenne muscular dystrophy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Toxicologic effects of an oligodeoxynucleotide phosphorothioate and its analogs following intravenous administration in rats

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Importance of nucleotide sequence and chemical modifications of antisense oligonucleotides

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Morpholino antisense oligomers: design, preparation, and properties

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Potent and nontoxic antisense oligonucleotides containing locked nucleic acids

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Antisense properties of peptide nucleic acid

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

In vivo metabolic profile of a phosphorothioate oligodeoxyribonucleotide

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

The molecular basis of muscular dystrophy in the mdx mouse: a point mutation

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Reconstruction of the 2.4 Mb human DMD-gene by homologous YAC recombination

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

Improved Fluorescence Method for Identifying Sex Chromatin in Formalin-fixed Tissue

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.031

10.1016/J.YMTHE.2004.05.031

7 January 2021

Identifiers

DOI

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8 December 2017

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