(Q45417049)

14 December 2017

title

Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia. (English)

1 reference

14 December 2017

0 references

0 references

glycogen storage disease

1 reference

Koeberl DD

1

1 reference

14 December 2017

Sun BD

2

1 reference

14 December 2017

Damodaran TV

3

1 reference

14 December 2017

Brown T

4

1 reference

14 December 2017

Millington DS

5

1 reference

14 December 2017

Benjamin DK Jr

6

1 reference

14 December 2017

Bird A

7

1 reference

14 December 2017

Schneider A

8

1 reference

14 December 2017

Hillman S

9

1 reference

14 December 2017

Jackson M

10

1 reference

14 December 2017

Beaty RM

11

1 reference

14 December 2017

Chen YT

12

1 reference

14 December 2017

publication date

4 May 2006

1 reference

14 December 2017

1 reference

14 December 2017

volume

13

1 reference

14 December 2017

issue

17

1 reference

14 December 2017

page(s)

1281-1289

1 reference

Glycogen storage disease in adults

14 December 2017

cites work

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Glucose-6-phosphatase dependent substrate transport in the glycogen storage disease type-1a mouse

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Correction of glycogen storage disease type 1a in a mouse model by gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Sustained hepatic and renal glucose-6-phosphatase expression corrects glycogen storage disease type Ia in mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Delivery of glucose-6-phosphatase in a canine model for glycogen storage disease, type Ia, with adeno-associated virus (AAV) vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Perturbation of fuel homeostasis caused by overexpression of the glucose-6-phosphatase catalytic subunit in liver of normal rats

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Unrestricted hepatocyte transduction with adeno-associated virus serotype 8 vectors in mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Efficacy of an adeno-associated virus 8-pseudotyped vector in glycogen storage disease type II.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Long-term correction of murine glycogen storage disease type Ia by recombinant adeno-associated virus-1-mediated gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Canine model and genomic structural organization of glycogen storage disease type Ia (GSD Ia).

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Liver transplantation for type I and type IV glycogen storage disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Long-term outcome of liver transplantation in patients with glycogen storage disease type Ia.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Liver transplantation for glycogen storage disease types I, III, and IV

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Type I glycogen storage disease: kidney involvement, pathogenesis and its treatment

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Single-gene disorders: what role could moonlighting enzymes play?

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

New nuclear functions of the glycolytic protein, glyceraldehyde-3-phosphate dehydrogenase, in mammalian cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

New insights into an old protein: the functional diversity of mammalian glyceraldehyde-3-phosphate dehydrogenase.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Hepatocellular carcinoma in glycogen storage disease type Ia: a case series

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

DNA-dependent PK inhibits adeno-associated virus DNA integration

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Evasion of immune responses to introduced human acid alpha-glucosidase by liver-restricted expression in glycogen storage disease type II.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Correction of glycogen storage disease type II by an adeno-associated virus vector containing a muscle-specific promoter

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Glycogen storage disease type Ia in two littermate Maltese puppies.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

Pulmonary hypertension in glycogen storage disease type I

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

7 January 2021

A new mutation of the glucose-6-phosphatase gene in a 4-year-old girl with oligosymptomatic glycogen storage disease type 1a

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

7 January 2021

Orthotopic liver transplantation for type I glycogenosis unresponsive to medical therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

7 January 2021

Liver transplantation for type I glycogen storage disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

7 January 2021

Amelioration of proximal renal tubular dysfunction in type I glycogen storage disease with dietary therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

7 January 2021

Nuclear translocation of GAPDH-GFP fusion protein during apoptosis

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

7 January 2021

Transduction by adeno-associated virus vectors in the rabbit airway: efficiency, persistence, and readministration.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

7 January 2021

Effect of continuous glucose therapy begun in infancy on the long-term clinical course of patients with type I glycogen storage disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

7 January 2021

Quantification of murine cytokine mRNAs using real time quantitative reverse transcriptase PCR

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302774

7 January 2021

Identifiers

DOI

10.1038/SJ.GT.3302774

1 reference

Dimensions Publication ID

14 December 2017

1018002686

0 references

1 reference