(Q45862016)

English

Packaging of an AAV vector encoding human acid α-glucosidase for gene therapy in glycogen storage disease type II with a modified hybrid adenovirus-AAV vector

scientific article published on April 1, 2003

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scholarly article

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

Packaging of an AAV vector encoding human acid α-glucosidase for gene therapy in glycogen storage disease type II with a modified hybrid adenovirus-AAV vector (English)

reason for preferred rank

most precise value

1 reference

10.1016/S1525-0016(03)00022-4

https://api.crossref.org/works/10.1016/S1525-0016(03)00022-4

29 December 2023

Packaging of an AAV vector encoding human acid alpha-glucosidase for gene therapy in glycogen storage disease type II with a modified hybrid adenovirus-AAV vector (English)

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727109

29 December 2023

vector-borne disease

0 references

0 references

1 reference

based on heuristic

inferred from title

glycogen storage disease

1 reference

based on heuristic

inferred from title

1 reference

10.1016/S1525-0016(03)00022-4

https://api.crossref.org/works/10.1016/S1525-0016(03)00022-4

29 December 2023

1 reference

10.1016/S1525-0016(03)00022-4

https://api.crossref.org/works/10.1016/S1525-0016(03)00022-4

29 December 2023

molecular medicine

1 reference

10.1016/S1525-0016(03)00022-4

https://api.crossref.org/works/10.1016/S1525-0016(03)00022-4

29 December 2023

author name string

Baodong Sun

1

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

Y-T Chen

2

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

Andrew Bird

3

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

Fang Xu

4

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

Yang-Xun Hou

5

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

Andrea Amalfitano

6

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

Dwight D. Koeberl

7

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727109

29 December 2023

language of work or name

1 reference

National Center for Biotechnology Information

PubMed publication ID

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=12727109

29 December 2023

publication date

1 April 2003

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

full work available at URL

http://www.cell.com/article/S1525001603000224/pdf

Portable Document Format

online access status

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A12727109

29 December 2023

https://api.elsevier.com/content/article/PII:S1525001603000224?httpAccept=text/xml

1 reference

10.1016/S1525-0016(03)00022-4

https://api.crossref.org/works/10.1016/S1525-0016(03)00022-4

29 December 2023

https://api.elsevier.com/content/article/PII:S1525001603000224?httpAccept=text/plain

1 reference

10.1016/S1525-0016(03)00022-4

https://api.crossref.org/works/10.1016/S1525-0016(03)00022-4

29 December 2023

Molecular Therapy

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

7

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

4

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

467-477

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

Novel tools for production and purification of recombinant adenoassociated virus vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Cell lines for the production of recombinant adeno-associated virus

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

A new strategy for large-scale preparation of high-titer recombinant adeno-associated virus vectors by using packaging cell lines and sulfonated cellulose column chromatography

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Packaging cells based on inducible gene amplification for the production of adeno-associated virus vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

High-titer adeno-associated viral vectors from a Rep/Cap cell line and hybrid shuttle virus

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Production of recombinant adeno-associated virus vectors using a packaging cell line and a hybrid recombinant adenovirus

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Targeted disruption of the acid alpha-glucosidase gene in mice causes an illness with critical features of both infantile and adult human glycogen storage disease type II

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Systemic correction of the muscle disorder glycogen storage disease type II after hepatic targeting of a modified adenovirus vector encoding human acid-alpha-glucosidase

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Long-term efficacy after [E1-, polymerase-] adenovirus-mediated transfer of human acid-alpha-glucosidase gene into glycogen storage disease type II knockout mice

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Intercellular transfer of the virally derived precursor form of acid alpha-glucosidase corrects the enzyme deficiency in inherited cardioskeletal myopathy Pompe disease

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Adeno-associated viral vector-mediated gene transfer results in long-term enzymatic and functional correction in multiple organs of Fabry mice

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

A simplified system for generating recombinant adenoviruses

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Production and characterization of improved adenovirus vectors with the E1, E2b, and E3 genes deleted

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Improved adeno-associated virus vector production with transfection of a single helper adenovirus gene, E4orf6.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Role for highly regulated rep gene expression in adeno-associated virus vector production

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Adeno-associated virus vectors can be efficiently produced without helper virus

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Efficacy of gene therapy for a prototypical lysosomal storage disease (GSD-II) is critically dependent on vector dose, transgene promoter, and the tissues targeted for vector transduction

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Conditional tissue-specific expression of the acid alpha-glucosidase (GAA) gene in the GAA knockout mice: implications for therapy

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Adeno-associated virus type 6 (AAV6) vectors mediate efficient transduction of airway epithelial cells in mouse lungs compared to that of AAV2 vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

An adenovirus type 5 mutant with the preterminal protein gene deleted efficiently provides helper functions for the production of recombinant adeno-associated virus

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Site-specific integration mediated by a hybrid adenovirus/adeno-associated virus vector.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Integrating adenovirus-adeno-associated virus hybrid vectors devoid of all viral genes.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

A high-capacity, capsid-modified hybrid adenovirus/adeno-associated virus vector for stable transduction of human hematopoietic cells

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Generation of recombinant adeno-associated virus vectors by a complete adenovirus-mediated approach

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Canine model and genomic structural organization of glycogen storage disease type Ia (GSD Ia).

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Isolation and characterization of packaging cell lines that coexpress the adenovirus E1, DNA polymerase, and preterminal proteins: implications for gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

High-level production of recombinant human lysosomal acid alpha-glucosidase in Chinese hamster ovary cells which targets to heart muscle and corrects glycogen accumulation in fibroblasts from patients with Pompe disease

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Introns increase transcriptional efficiency in transgenic mice

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Persistent expression of human clotting factor IX from mouse liver after intravenous injection of adeno-associated virus vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Delivery of glucose-6-phosphatase in a canine model for glycogen storage disease, type Ia, with adeno-associated virus (AAV) vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Multiply deleted [E1, polymerase-, and pTP-] adenovirus vector persists despite deletion of the preterminal protein

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Quantification of murine cytokine mRNAs using real time quantitative reverse transcriptase PCR

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900022-4

7 January 2021

based on heuristic

inferred from DOI database lookup

Use of Adeno-Associated Virus as a General Transduction Vector for Mammalian Cells

1

1 reference

10.1016/S1525-0016(03)00022-4

https://api.crossref.org/works/10.1016/S1525-0016(03)00022-4

29 December 2023

Increased apoptosis of Huntington disease lymphoblasts associated with repeat length-dependent mitochondrial depolarization

15

1 reference

10.1016/S1525-0016(03)00022-4

https://api.crossref.org/works/10.1016/S1525-0016(03)00022-4

29 December 2023

Identifiers

10.1016/S1525-0016(03)00022-4

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

PubMed publication ID

1 reference

Europe PubMed Central

PubMed publication ID

17 December 2017

http://europepmc.org/abstract/MED/12727109

ResearchGate publication ID

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