(Q45868873)

17 December 2017

title

High-level factor VIII gene expression in vivo achieved by nonviral liver-specific gene therapy vectors (English)

1 reference

17 December 2017

High-Level Factor VIII Gene ExpressionIn VivoAchieved by Nonviral Liver-Specific Gene Therapy Vectors (English)

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

13 March 2024

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14503965

13 March 2024

gene expression

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14503965

13 March 2024

genetic vector

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14503965

13 March 2024

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

13 March 2024

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

13 March 2024

author name string

Xin Ye

2

1 reference

17 December 2017

Carol H. Miao

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14503965

13 March 2024

Arthur R. Thompson

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14503965

13 March 2024

language of work or name

English

1 reference

National Center for Biotechnology Information

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=14503965

13 March 2024

publication date

1 September 2003

1 reference

17 December 2017

20 September 2003

1 reference

National Center for Biotechnology Information

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=14503965

full work available at URL

13 March 2024

http://www.liebertpub.com/doi/pdf/10.1089/104303403322319381

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

13 March 2024

1 reference

17 December 2017

volume

14

1 reference

17 December 2017

issue

14

1 reference

17 December 2017

page(s)

1297-1305

1 reference

17 December 2017

Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A.

cites work

2

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors

13 March 2024

4

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

LCR-mediated, long-term tissue-specific gene expression within replicating episomal plasmid and cosmid vectors

13 March 2024

5

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Cell-specific expression of a transfected human alpha 1-antitrypsin gene

13 March 2024

6

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

In vivo footprinting analysis of the hepatic control region of the human apolipoprotein E/C-I/C-IV/C-II gene locus

13 March 2024

7

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Purification of a novel protein (ps20) from urogenital sinus mesenchymal cells with growth inhibitory properties in vitro

13 March 2024

8

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Expression of factor VIII by murine liver sinusoidal endothelial cells

13 March 2024

9

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Development of catheter-based procedures for transducing the isolated rabbit liver with plasmid DNA.

13 March 2024

10

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

The beta-globin locus control region versus gene therapy vectors: a struggle for expression.

13 March 2024

11

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Gene therapy for the treatment of hemophilia B using PINC-formulated plasmid delivered to muscle with electroporation

13 March 2024

12

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Upstream and intronic regulatory sequences interact in the activation of the glutamine synthetase promoter

13 March 2024

14

1 reference

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Regulatory functions of 3'UTRs.

13 March 2024

17

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy

13 March 2024

18

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Immune evasion by muscle-specific gene expression in dystrophic muscle

13 March 2024

19

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Analysis of muscle creatine kinase regulatory elements in recombinant adenoviral vectors

13 March 2024

20

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Locus control region of the human CD2 gene in a lentivirus vector confers position-independent transgene expression

13 March 2024

24

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Use of blood outgrowth endothelial cells for gene therapy for hemophilia A.

13 March 2024

25

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Hydrodynamics-based transfection in animals by systemic administration of plasmid DNA.

13 March 2024

26

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Sequences in the coding region of clotting factor VIII act as dominant inhibitors of RNA accumulation and protein production.

13 March 2024

27

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Inclusion of the hepatic locus control region, an intron, and untranslated region increases and stabilizes hepatic factor IX gene expression in vivo but not in vitro

13 March 2024

28

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Long-term and therapeutic-level hepatic gene expression of human factor IX after naked plasmid transfer in vivo

13 March 2024

29

1 reference

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Global non-viral gene transfer to the primate brain following intravenous administration.

13 March 2024

30

1 reference

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In vitro polyadenylation is stimulated by the presence of an upstream intron

13 March 2024

31

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

The canine factor VIII 3'-untranslated region and a concatemeric hepatocyte nuclear factor 1 regulatory element enhance factor VIII transgene expression in vivo

13 March 2024

32

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Sustained human factor VIII expression in hemophilia A mice following systemic delivery of a gutless adenoviral vector

13 March 2024

33

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A.

13 March 2024

34

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Targeted transfection by femtosecond laser

13 March 2024

35

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Exploration of structure-function relationships in human factor VIII by site-directed mutagenesis

13 March 2024

36

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice

13 March 2024

37

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Construction of human factor IX expression vectors in retroviral vector frames optimized for muscle cells

13 March 2024

38

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

Complete and sustained phenotypic correction of hemophilia B in mice following hepatic gene transfer of a high-expressing human factor IX plasmid

13 March 2024

39

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

High levels of foreign gene expression in hepatocytes after tail vein injections of naked plasmid DNA.

13 March 2024

40

1 reference

https://api.crossref.org/works/10.1089/104303403322319381

13 March 2024

Identifiers

1 reference

17 December 2017

1 reference

17 December 2017