(Q45871954)

17 December 2017

title

Successful ex vivo gene therapy directed to liver in a patient with familial hypercholesterolaemia (English)

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17 December 2017

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7

Lupien PJ

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17 December 2017

author name string

Grossman M

1

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17 December 2017

Raper SE

2

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17 December 2017

Kozarsky K

3

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17 December 2017

Stein EA

4

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17 December 2017

Engelhardt JF

5

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17 December 2017

Muller D

6

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17 December 2017

Wilson JM

8

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17 December 2017

language of work or name

English

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publication date

1 April 1994

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17 December 2017

published in

Nature Genetics

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17 December 2017

volume

6

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17 December 2017

page(s)

335-341

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17 December 2017

issue

4

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17 December 2017

https://scigraph.springernature.com/pub.10.1038/ng0494-335

exact match

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cites work

Heart-liver transplantation in a patient with familial hypercholesterolaemia

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

Liver transplantation to provide low-density-lipoprotein receptors and lower plasma cholesterol in a child with homozygous familial hypercholesterolemia

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

42 bp element from LDL receptor gene confers end-product repression by sterols when inserted into viral TK promoter

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

A receptor-mediated pathway for cholesterol homeostasis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Long-Term Improvement of Hypercholesterolemia After Ex Vivo Gene Therapy in LDLR-Deficient Rabbits

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Transplantation of genetically modified autologous hepatocytes into nonhuman primates: feasibility and short-term toxicity.

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Common low-density lipoprotein receptor mutations in the French Canadian population

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Ex vivo gene therapy of familial hypercholesterolemia.

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Expression of human factor IX in rabbit hepatocytes by retrovirus-mediated gene transfer: potential for gene therapy of hemophilia B.

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Expression of human alpha 1-antitrypsin in dogs after autologous transplantation of retroviral transduced hepatocytes

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Adenovirus-mediated in vivo gene transfer and expression in normal rat liver

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Increased expression of DNA cointroduced with nuclear protein in adult rat liver

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Towards liver-directed gene therapy: retrovirus-mediated gene transfer into human hepatocytes

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Submucosal glands are the predominant site of CFTR expression in the human bronchus

1 reference

https://api.crossref.org/works/10.1038%2FNG0494-335

7 January 2021

Identifiers

DOI

10.1038/NG0494-335

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17 December 2017

Dimensions Publication ID

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17 December 2017