(Q45872484)
Statements
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Hematopoietic stem cell gene therapy leads to marked visceral organ improvements and a delayed onset of neurological abnormalities in the acid sphingomyelinase deficient mouse model of Niemann-Pick disease (English)
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Schuchman EH
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Miranda SR
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Erlich S
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Friedrich VL Jr
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Gatt S
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1 October 2000
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7
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20
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1768-1776
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Identifiers
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