(Q46449770)

English

Ex vivo gene editing of the dystrophin gene in muscle stem cells mediated by peptide nucleic acid single stranded oligodeoxynucleotides induces stable expression of dystrophin in a mouse model for Duchenne muscular dystrophy

scientific article published in July 2014

In more languages

default for all languages

No label defined

No description defined

Statements

scholarly article

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

Ex vivo gene editing of the dystrophin gene in muscle stem cells mediated by peptide nucleic acid single stranded oligodeoxynucleotides induces stable expression of dystrophin in a mouse model for Duchenne muscular dystrophy (English)

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

peptide nucleic acid

1 reference

based on heuristic

inferred from title

author name string

Farnoosh Nik-Ahd

1

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

Carmen Bertoni

2

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

publication date

1 July 2014

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

32

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

7

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

1817-1830

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

Isolation of candidate cDNAs for portions of the Duchenne muscular dystrophy gene

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Complete cloning of the duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Dystrophin: the protein product of the Duchenne muscular dystrophy locus

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Specific removal of the nonsense mutation from the mdx dystrophin mRNA using antisense oligonucleotides.

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Dystrophin gene repair in mdx muscle precursor cells in vitro and in vivo mediated by RNA-DNA chimeric oligonucleotides

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Strand bias in oligonucleotide-mediated dystrophin gene editing

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Clinical approaches in the treatment of Duchenne muscular dystrophy (DMD) using oligonucleotides

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Site-directed gene repair of the dystrophin gene mediated by PNA-ssODNs

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

PTC124 targets genetic disorders caused by nonsense mutations

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Read-through compound 13 restores dystrophin expression and improves muscle function in the mdx mouse model for Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Nonaminoglycoside compounds induce readthrough of nonsense mutations

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Enhancement of plasmid-mediated gene therapy for muscular dystrophy by directed plasmid integration.

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

T and B lymphocyte depletion has a marked effect on the fibrosis of dystrophic skeletal muscles in the scid/mdx mouse

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Satellite cell of skeletal muscle fibers

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

The regulation of Notch signaling controls satellite cell activation and cell fate determination in postnatal myogenesis.

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Preparation of adult muscle fiber-associated stem/precursor cells

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Increased Wnt signaling during aging alters muscle stem cell fate and increases fibrosis

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Long-term persistence and migration of myogenic cells injected into pre-irradiated muscles of mdx mice

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Stem cell function, self-renewal, and behavioral heterogeneity of cells from the adult muscle satellite cell niche.

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Myotoxic phospholipases A2 and the regeneration of skeletal muscles

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Donor satellite cell engraftment is significantly augmented when the host niche is preserved and endogenous satellite cells are incapacitated

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

A high-content, high-throughput siRNA screen identifies cyclin D2 as a potent regulator of muscle progenitor cell fusion and a target to enhance muscle regeneration

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Rescue of dystrophin expression in mdx mouse muscle by RNA/DNA oligonucleotides

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

A new blocking method for application of murine monoclonal antibody to mouse tissue sections

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Restoration of dystrophin expression in mdx muscle cells by chimeraplast-mediated exon skipping

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

A new mathematical model for relative quantification in real-time RT-PCR

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Enhanced gene repair mediated by methyl-CpG-modified single-stranded oligonucleotides

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Properties of isolated adult rat muscle fibres maintained in tissue culture

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Proliferation of muscle satellite cells on intact myofibers in culture

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Autologous transplantation of SM/C-2.6(+) satellite cells transduced with micro-dystrophin CS1 cDNA by lentiviral vector into mdx mice.

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Conversion of mdx myofibres from dystrophin-negative to -positive by injection of normal myoblasts

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Somatic reversion/suppression of the mouse mdx phenotype in vivo.

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Successful histocompatible myoblast transplantation in dystrophin-deficient mdx mouse despite the production of antibodies against dystrophin.

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

The fate of individual myoblasts after transplantation into muscles of DMD patients

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

The fate of myoblasts following transplantation into mature muscle

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Highly efficient, functional engraftment of skeletal muscle stem cells in dystrophic muscles

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Self-renewal and expansion of single transplanted muscle stem cells

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Prevention of muscle aging by myofiber-associated satellite cell transplantation

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

A subpopulation of adult skeletal muscle stem cells retains all template DNA strands after cell division

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Transduction of skeletal muscles with common reporter genes can promote muscle fiber degeneration and inflammation

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Muscle precursor cells injected into irradiated mdx mouse muscle persist after serial injury.

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Sprouty1 regulates reversible quiescence of a self-renewing adult muscle stem cell pool during regeneration

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Direct isolation of satellite cells for skeletal muscle regeneration

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Pericytes of human skeletal muscle are myogenic precursors distinct from satellite cells

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Immunohistological intensity measurements as a tool to assess sarcolemma-associated protein expression

1 reference

https://api.crossref.org/works/10.1002%2FSTEM.1668

21 January 2018

Identifiers

10.1002/STEM.1668

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

PubMed publication ID

1 reference

Europe PubMed Central

PubMed publication ID

22 December 2017

http://europepmc.org/abstract/MED/24753122

Sitelinks

Wikipedia(0 entries)

Wikibooks(0 entries)

Wikinews(0 entries)

Wikiquote(0 entries)

Wikisource(0 entries)

Wikiversity(0 entries)

Wikivoyage(0 entries)

Wiktionary(0 entries)

Multilingual sites(0 entries)

Retrieved from "https://www.wikidata.org/w/index.php?title=Q46449770&oldid=2112048597"