(Q48396355)
Statements
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Enzyme replacement therapy in two patients with an advanced severe (Hurler) phenotype of mucopolysaccharidosis I. (English)
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Ingeborg Barisic
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Visnja Tokic
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Nevenka Huzjak
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Giorgie Petkovic
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Ksenija Fumic
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Eduard Paschke
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17 October 2006
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166
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7
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727-732
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