(Q50004193)
Statements
1 reference
Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy. (English)
1 reference
Claudia A Chiriboga
John W Day
Craig Campbell
Anne M Connolly
Nancy L Kuntz
Kayoko Saito
Perry B Shieh
Már Tulinius
Elena S Mazzone
Jacqueline Montes
Kathie M Bishop
Qingqing Yang
Richard Foster
Sarah Gheuens
C Frank Bennett
Wildon Farwell
Eugene Schneider
Darryl C De Vivo
Richard S Finkel
CHERISH Study Group
1 February 2018
1 reference