(Q52604772)
Statements
Dose-Dependent Lowering of Mutant Huntingtin Using Antisense Oligonucleotides in Huntington Disease Patients. (English)
Raymund A C Roos
Willeke M C van Roon-Mom
Susanne T de Bot
13 March 2018
28
2
59-62
scientific article published on 13 March 2018