(Q53968058)
Statements
Correlation of bone marrow response with hematological, biochemical, and visceral responses to enzyme replacement therapy of nonneuronopathic (type 1) Gaucher disease in 30 adult patients (English)
Dieter Häussinger
Ludger Wilhelm Poll
Jens-Albrecht Koch
Reinhart Willers
Axel Scherer
Ulrich Mödder
Stephan vom Dahl