(Q56482184)

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

A multiinstitutional survey of the Wiskott-Aldrich syndrome.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Autoimmunity in Wiskott-Aldrich syndrome: risk factors, clinical features, and outcome in a single-center cohort of 55 patients

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Clinical course of patients with WASP gene mutations

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Mutations of the Wiskott-Aldrich Syndrome Protein (WASP): hotspots, effect on transcription, and translation and phenotype/genotype correlation

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Genotype-proteotype linkage in the Wiskott-Aldrich syndrome

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

The Wiskott-Aldrich syndrome protein: forging the link between actin and cell activation

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Mechanisms of WASp-mediated hematologic and immunologic disease.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

The identification and characterization of two promoters and the complete genomic sequence for the Wiskott-Aldrich syndrome gene

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Lentiviral vector-mediated gene transfer in T cells from Wiskott-Aldrich syndrome patients leads to functional correction.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Lentiviral vectors transcriptionally targeted to hematopoietic cells by WASP gene proximal promoter sequences.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Interaction of the Wiskott-Aldrich syndrome protein with sorting nexin 9 is required for CD28 endocytosis and cosignaling in T cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

A role for Wiskott-Aldrich syndrome protein in T-cell receptor-mediated transcriptional activation independent of actin polymerization

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

The Wiskott-Aldrich syndrome protein regulates nuclear translocation of NFAT2 and NF-kappa B (RelA) independently of its role in filamentous actin polymerization and actin cytoskeletal rearrangement.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Regulation of cytoskeletal dynamics at the immune synapse: new stars join the actin troupe

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Wiskott-Aldrich syndrome protein and the cytoskeletal dynamics of dendritic cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Wiskott-Aldrich syndrome protein regulates lipid raft dynamics during immunological synapse formation.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

NK cell activation by dendritic cells (DCs) requires the formation of a synapse leading to IL-12 polarization in DCs.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Defective Th1 cytokine gene transcription in CD4+ and CD8+ T cells from Wiskott-Aldrich syndrome patients.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Wiskott-Aldrich syndrome protein is required for regulatory T cell homeostasis

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

The Wiskott-Aldrich syndrome protein is required for the function of CD4(+)CD25(+)Foxp3(+) regulatory T cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

WASP regulates suppressor activity of human and murine CD4(+)CD25(+)FOXP3(+) natural regulatory T cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Impaired in vitro regulatory T cell function associated with Wiskott-Aldrich syndrome

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Impaired signaling via the high-affinity IgE receptor in Wiskott-Aldrich syndrome protein-deficient mast cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

WASP deficiency leads to global defects of directed leukocyte migration in vitro and in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Deficiency in the Wiskott-Aldrich protein induces premature proplatelet formation and platelet production in the bone marrow compartment

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Successful reconstitution of immunity in ADA-SCID by stem cell gene therapy following cessation of PEG-ADA and use of mild preconditioning

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Retrovirus-mediated WASP gene transfer corrects defective actin polymerization in B cell lines from Wiskott-Aldrich syndrome patients carrying 'null' mutations.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Functional correction of T cells derived from patients with the Wiskott–Aldrich syndrome (WAS) by transduction with an oncoretroviral vector encoding the WAS protein

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

A lentiviral vector encoding the human Wiskott-Aldrich syndrome protein corrects immune and cytoskeletal defects in WASP knockout mice.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Retroviral WASP gene transfer into human hematopoietic stem cells reconstitutes the actin cytoskeleton in myeloid progeny cells differentiated in vitro.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Wiskott-Aldrich syndrome protein-deficient mice reveal a role for WASP in T but not B cell activation

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Antigen receptor-induced activation and cytoskeletal rearrangement are impaired in Wiskott-Aldrich syndrome protein-deficient lymphocytes

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Gene therapy for Wiskott-Aldrich syndrome: rescue of T-cell signaling and amelioration of colitis upon transplantation of retrovirally transduced hematopoietic stem cells in mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Efficacy of gene therapy for Wiskott-Aldrich syndrome using a WAS promoter/cDNA-containing lentiviral vector and nonlethal irradiation.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

A defect in hematopoietic stem cell migration explains the nonrandom X-chromosome inactivation in carriers of Wiskott-Aldrich syndrome

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Somatic mosaicism in Wiskott--Aldrich syndrome suggests in vivo reversion by a DNA slippage mechanism.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Mosaicism of NK cells in a patient with Wiskott-Aldrich syndrome

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Mutagenesis and oncogenesis by chromosomal insertion of gene transfer vectors.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Cell-culture assays reveal the importance of retroviral vector design for insertional genotoxicity

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Insertional mutagenesis in gene therapy and stem cell biology

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Transcription start regions in the human genome are favored targets for MLV integration

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Stem cell gene transfer: insights into integration and hematopoiesis from primate genetic marking studies

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Promoter trapping reveals significant differences in integration site selection between MLV and HIV vectors in primary hematopoietic cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Retrovirus-mediated gene transfer into embryonal carcinoma and hemopoietic stem cells: expression from a hybrid long terminal repeat

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Viral vectors for gene therapy: the art of turning infectious agents into vehicles of therapeutics

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Development of a sensitive assay for detection of replication-competent recombinant lentivirus in large-scale HIV-based vector preparations

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Lentiviral vector integration sites in human NOD/SCID repopulating cells.

21 January 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Hot spots of retroviral integration in human CD34+ hematopoietic cells

21 January 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2789278

Development of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome.

29 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2789278

Wiskott-Aldrich syndrome protein is involved in alphaIIb beta3-mediated cell adhesion

29 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2789278

Gene therapy: great expectations?

29 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2789278

Self-inactivating lentivirus vector for safe and efficient in vivo gene delivery

29 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2789278

A 5' regulatory sequence containing two Ets motifs controls the expression of the Wiskott-Aldrich syndrome protein (WASP) gene in human hematopoietic cells.

29 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2789278

Expression of Wiskott-Aldrich syndrome protein (WASP) gene during hematopoietic differentiation.

29 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2789278

Splenectomy and/or bone marrow transplantation in the management of the Wiskott-Aldrich syndrome: long-term follow-up of 62 cases

29 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2789278

Long-term outcome following hematopoietic stem-cell transplantation in Wiskott-Aldrich syndrome: collaborative study of the European Society for Immunodeficiencies and European Group for Blood and Marrow Transplantation

29 September 2018

1 reference

https://api.crossref.org/works/10.1517%2F14712598.8.2.181

Correction of the murine Wiskott-Aldrich syndrome phenotype by hematopoietic stem cell transplantation

21 January 2018

1 reference

12 December 2020

Lentiviral gene transfer and ex vivo expansion of human primitive stem cells capable of primary, secondary, and tertiary multilineage repopulation in NOD/SCID mice. Nonobese diabetic/severe combined immunodeficient

1 reference

12 December 2020

High incidence of lymphomas in a subgroup of wiskott–aldrich syndrome patients

1 reference

12 December 2020

Differential contribution of Wiskott-Aldrich syndrome protein to selective advantage in T- and B-cell lineages

1 reference

12 December 2020

The Wiskott-Aldrich syndrome

1 reference

12 December 2020