(Q63197217)
English
Enzyme replacement therapy for mucopolysaccharidosis VI: A phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, o
scientific article published on 01 April 2006
Statements
Enzyme replacement therapy for mucopolysaccharidosis VI: a phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study (English)
Ida Schwartz
Roberto Giugliani
Paul Harmatz
Nathalie Guffon
Elisa Leão Teles
Stuart J Swiedler
J Edmond Wraith
Laila Arash
Maurizio Scarpa
Michael Beck
Zi-Fan Yu
Emil Kakkis
M Clara Sá Miranda
Janet Wittes
Mary S Newman
Ann M Lowe
MPS VI Phase 3 Study Group