(Q90466184)
Statements
Discovery of Risdiplam, a Selective Survival of Motor Neuron-2 ( SMN2) Gene Splicing Modifier for the Treatment of Spinal Muscular Atrophy (SMA) (English)
John Baird
Stefanie Bendels
Johan Bylund
Karen S Chen
Nora Denk
Zhihua Feng
Luke Green
Melanie Guerard
Philippe Jablonski
Bjoern Jacobsen
Omar Khwaja
Heidemarie Kletzl
Chien-Ping Ko
Stefan Kustermann
Anne Marquet
Friedrich Metzger
Barbara Mueller
Nikolai A Naryshkin
Sergey V Paushkin
Emmanuel Pinard
Agnès Poirier
Michael Reutlinger
Marla Weetall
Andreas Zeller
Xin Zhao