(Q34224260)

31 July 2017

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title

From gene transfer to gene therapy in lysosomal storage diseases affecting the central nervous system (English)

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31 July 2017

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Poenaru L

1

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31 July 2017

language of work or name

English

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publication date

1 February 2001

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31 July 2017

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31 July 2017

volume

33

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31 July 2017

issue

1

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31 July 2017

page(s)

28-36

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Lysosomal storage diseases

31 July 2017

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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In utero gene therapy: transfer and long-term expression of the bacterial neo(r) gene in sheep after direct injection of retroviral vectors into preimmune fetuses

21 January 2018

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Gene therapy for canine alpha-L-iduronidase deficiency: in utero adoptive transfer of genetically corrected hematopoietic progenitors results in engraftment but not amelioration of disease

21 January 2018

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21 January 2018

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21 January 2018

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Gene transfer approaches to the lysosomal storage disorders

21 January 2018

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Correction of the UDP-glucuronosyltransferase gene defect in the gunn rat model of crigler-najjar syndrome type I with a chimeric oligonucleotide

21 January 2018

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10.3109/07853890109002057

21 January 2018

Identifiers

DOI

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31 July 2017

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