(Q34393866)

1 August 2017

title

Permanent and panerythroid correction of murine beta thalassemia by multiple lentiviral integration in hematopoietic stem cells (English)

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1 August 2017

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14

Philippe Leboulch

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1 August 2017

6

Connie J Eaves

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1 August 2017

Suzan Imren

1

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1 August 2017

Emmanuel Payen

2

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1 August 2017

Karen A Westerman

3

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1 August 2017

Robert Pawliuk

4

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1 August 2017

Mary E Fabry

5

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1 August 2017

Benjamin Cavilla

7

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1 August 2017

Louis D Wadsworth

8

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1 August 2017

Yves Beuzard

9

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1 August 2017

Eric E Bouhassira

10

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1 August 2017

Robert Russell

11

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1 August 2017

Irving M London

12

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1 August 2017

Ronald L Nagel

13

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1 August 2017

R Keith Humphries

15

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1 August 2017

language of work or name

English

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publication date

21 October 2002

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Proceedings of the National Academy of Sciences of the United States of America

1 August 2017

published in

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1 August 2017

volume

99

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1 August 2017

issue

22

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1 August 2017

page(s)

14380-14385

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Stochastic gene expression in a single cell

1 August 2017

cites work

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Correction of sickle cell disease in transgenic mouse models by gene therapy

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Preselection of retrovirally transduced bone marrow avoids subsequent stem cell gene silencing and age-dependent extinction of expression of human beta-globin in engrafted mice.

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

The protein CTCF is required for the enhancer blocking activity of vertebrate insulators

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

6 July 2018

The beta-thalassemias

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Thalassemia--a global public health problem

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Mutagenesis of retroviral vectors transducing human beta-globin gene and beta-globin locus control region derivatives results in stable transmission of an active transcriptional structure

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Generation of a high-titer retroviral vector capable of expressing high levels of the human beta-globin gene

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Mapping of DNase I-hypersensitive sites in the upstream DNA of human embryonic epsilon-globin gene in K562 leukemia cells

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

The "beta-like-globin" gene domain in human erythroid cells

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Position-independent, high-level expression of the human beta-globin gene in transgenic mice

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

An erythroid-specific, developmental-stage-independent enhancer far upstream of the human "beta-like globin" genes

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

High-level beta-globin expression after retroviral transfer of locus activation region-containing human beta-globin gene derivatives into murine erythroleukemia cells

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

A 36-base-pair core sequence of locus control region enhances retrovirally transferred human beta-globin gene expression

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

High expression of human beta S- and alpha-globins in transgenic mice: erythrocyte abnormalities, organ damage, and the effect of hypoxia

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Anti-beta s-ribozyme reduces beta s mRNA levels in transgenic mice: potential application to the gene therapy of sickle cell anemia

6 July 2018

1 reference

Crossref

https://api.crossref.org/works/10.1073%2FPNAS.212507099

Genetic correction of sickle cell disease: insights using transgenic mouse models

21 January 2018

1 reference

Crossref

https://api.crossref.org/works/10.1073%2FPNAS.212507099

Functional requirements for phenotypic correction of murine beta-thalassemia: implications for human gene therapy

21 January 2018

1 reference

Crossref

https://api.crossref.org/works/10.1073%2FPNAS.212507099

Long-term transfer and expression of the human beta-globin gene in a mouse transplant model

21 January 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

Selection of retrovirally transduced hematopoietic cells using CD24 as a marker of gene transfer.

27 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=137892

27 October 2018

1 reference

12 December 2020

Successful treatment of murine beta-thalassemia intermedia by transfer of the human beta-globin gene

1 reference

12 December 2020

A mouse model for β-thalassemia

1 reference

12 December 2020

An objective sign in painful crisis in sickle cell anemia: the concomitant reduction of high density red cells

1 reference

12 December 2020

A study of membrane protein defects and alpha hemoglobin chains of red blood cells in human beta thalassemia

1 reference

12 December 2020

Transcriptional behavior of LCR enhancer elements integrated at the same chromosomal locus by recombinase-mediated cassette exchange

1 reference

12 December 2020

HIV-1 genome nuclear import is mediated by a central DNA flap

1 reference

12 December 2020

Identifiers

DOI

10.1073/PNAS.212507099

1 reference

1 August 2017

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1 August 2017

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