(Q34556098)

English

Safety and efficacy of olesoxime in patients with type 2 or non-ambulatory type 3 spinal muscular atrophy: a randomised, double-blind, placebo-controlled phase 2 trial.

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scholarly article

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Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Safety and efficacy of olesoxime in patients with type 2 or non-ambulatory type 3 spinal muscular atrophy: a randomised, double-blind, placebo-controlled phase 2 trial (English)

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

phase II clinical trial

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0 references

spinal muscular atrophy

1 reference

based on heuristic

inferred from title

muscular atrophy

1 reference

based on heuristic

inferred from title

1

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

2

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Eugenio Mercuri

3

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Janbernd Kirschner

5

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Anna Łusakowska

7

object named as

Anna Lusakowska

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

author name string

Francesco Muntoni

4

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Carol Reid

6

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Giacomo P Comi

8

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Jean-Marie Cuisset

9

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Jean-Louis Abitbol

10

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Bruno Scherrer

11

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Patricia Sanwald Ducray

12

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Jeppe Buchbjerg

13

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Eduardo Vianna

14

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

W Ludo van der Pol

15

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Carole Vuillerot

16

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Thomas Blaettler

17

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Paulo Fontoura

18

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Olesoxime SMA Phase 2 Study Investigators

19

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

publication date

28 April 2017

1 reference

Europe PubMed Central

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Lancet Neurology

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

16

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

7

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

513-522

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

Spinal muscular atrophy.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

The neurobiology of childhood spinal muscular atrophy.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Understanding the experiences and needs of individuals with Spinal Muscular Atrophy and their parents: a qualitative study

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Correlation between severity and SMN protein level in spinal muscular atrophy

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Mitochondrial dysfunction in a neural cell model of spinal muscular atrophy.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Mitochondrial dysfunction in neuromuscular disorders

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Impaired Muscle Mitochondrial Biogenesis and Myogenesis in Spinal Muscular Atrophy.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Motor neuron mitochondrial dysfunction in spinal muscular atrophy

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Spinal muscular atrophy: a motor neuron disorder or a multi-organ disease?

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Perspectives of drug-based neuroprotection targeting mitochondria.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

The activity of the spinal muscular atrophy protein is regulated during development and cellular differentiation.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Olesoxime (TRO19622): A Novel Mitochondrial-Targeted Neuroprotective Compound

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Olesoxime protects embryonic cortical neurons from camptothecin intoxication by a mechanism distinct from BDNF.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Protective role of olesoxime against wild-type α-synuclein-induced toxicity in human neuronally differentiated SHSY-5Y cells

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Identification and characterization of cholest-4-en-3-one, oxime (TRO19622), a novel drug candidate for amyotrophic lateral sclerosis

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

A phase II−III trial of olesoxime in subjects with amyotrophic lateral sclerosis

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

A motor function measure for neuromuscular diseases. Construction and validation study

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Motor function measure: validation of a short form for young children with neuromuscular diseases

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

The PedsQL in pediatric patients with Spinal Muscular Atrophy: feasibility, reliability, and validity of the Pediatric Quality of Life Inventory Generic Core Scales and Neuromuscular Module

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Responsiveness of the motor function measure in patients with spinal muscular atrophy

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Concerns about the design of clinical trials for spinal muscular atrophy

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials.

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Prospective study of spinal muscular atrophy before age 6 years. DCN/SMA Group

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Hammersmith Functional Motor Scale and Motor Function Measure-20 in non ambulant SMA patients

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

The motor neuron response to SMN1 deficiency in spinal muscular atrophy

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Characteristics and performance of a modified version of the ADCS-CGIC CIBIC+ for mild cognitive impairment clinical trials

1 reference

https://api.crossref.org/works/10.1016%2FS1474-4422%2817%2930085-6

7 January 2021

based on heuristic

inferred from DOI database lookup

Identifiers

10.1016/S1474-4422(17)30085-6

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

PubMed publication ID

1 reference

Europe PubMed Central

PubMed publication ID

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:28460889%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

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