(Q35678425)

9 August 2017

title

Novel mini-dystrophin gene dual adeno-associated virus vectors restore neuronal nitric oxide synthase expression at the sarcolemma (English)

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9 August 2017

0 references

Yadong Zhang

1

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9 August 2017

Dongsheng Duan

series ordinal

2

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9 August 2017

publication date

24 October 2011

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9 August 2017

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9 August 2017

volume

23

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9 August 2017

issue

1

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9 August 2017

page(s)

98-103

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Duchenne muscular dystrophy gene therapy: Lost in translation?

9 August 2017

cites work

1 reference

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Nitrosative stress elicited by nNOSµ delocalization inhibits muscle force in dystrophin-null mice

12 July 2018

1 reference

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Gene therapy of mdx mice with large truncated dystrophins generated by recombination using rAAV6.

12 July 2018

1 reference

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Efficient transgene reconstitution with hybrid dual AAV vectors carrying the minimized bridging sequences

12 July 2018

1 reference

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Adeno-associated virus serotype 6 capsid tyrosine-to-phenylalanine mutations improve gene transfer to skeletal muscle

12 July 2018

1 reference

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Sarcolemmal nNOS anchoring reveals a qualitative difference between dystrophin and utrophin.

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Mutational spectrum of DMD mutations in dystrophinopathy patients: application of modern diagnostic techniques to a large cohort

12 July 2018

1 reference

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Evidence for the failure of adeno-associated virus serotype 5 to package a viral genome > or = 8.2 kb.

12 July 2018

1 reference

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Persistent expression of FLAG-tagged micro dystrophin in nonhuman primates following intramuscular and vascular delivery

12 July 2018

1 reference

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Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy.

12 July 2018

1 reference

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Next generation of adeno-associated virus 2 vectors: point mutations in tyrosines lead to high-efficiency transduction at lower doses

12 July 2018

1 reference

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Expanding adeno-associated viral vector capacity: a tale of two vectors.

12 July 2018

1 reference

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A hybrid vector system expands adeno-associated viral vector packaging capacity in a transgene-independent manner

12 July 2018

1 reference

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From the smallest virus to the biggest gene: marching towards gene therapy for duchenne muscular dystrophy

12 July 2018

1 reference

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Viral serotype and the transgene sequence influence overlapping adeno-associated viral (AAV) vector-mediated gene transfer in skeletal muscle

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors

12 July 2018

1 reference

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2004 William Allan Award address. Cloning of the DMD gene

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Microdystrophin gene therapy of cardiomyopathy restores dystrophin-glycoprotein complex and improves sarcolemma integrity in the mdx mouse heart.

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Nitric oxide contributes to vascular smooth muscle relaxation in contracting fast-twitch muscles

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Impaired metabolic modulation of alpha-adrenergic vasoconstriction in dystrophin-deficient skeletal muscle

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Recombinant truncated dystrophin minigenes: construction, expression, and adenoviral delivery

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Nitric oxide synthase complexed with dystrophin and absent from skeletal muscle sarcolemma in Duchenne muscular dystrophy

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Molecular and phenotypic analysis of patients with deletions within the deletion-rich region of the Duchenne muscular dystrophy (DMD) gene

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

The molecular basis for Duchenne versus Becker muscular dystrophy: correlation of severity with type of deletion

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Exploring the molecular basis for variability among patients with Becker muscular dystrophy: dystrophin gene and protein studies

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

A highly functional mini-dystrophin/GFP fusion gene for cell and gene therapy studies of Duchenne muscular dystrophy

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy

25 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison

25 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3260444

Efficient recovery of dysferlin deficiency by dual adeno-associated vector-mediated gene transfer

25 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/21933029

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1089/HUM.2011.131

1 reference

9 August 2017

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9 August 2017

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