(Q36370817)

English

Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans.

scientific article

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scholarly article

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Europe PubMed Central

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:22968453%20AND%20SRC:MED&resulttype=core&format=json

13 February 2020

Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans (English)

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13 February 2020

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13 February 2020

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13 February 2020

Shepherd H Schurman

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13 February 2020

Chimene Kesserwan

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13 February 2020

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Gay M Crooks

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13 February 2020

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Fabio Candotti

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13 February 2020

Kit L Shaw

2

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13 February 2020

Linda Muul

3

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13 February 2020

Denise Carbonaro

4

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13 February 2020

Robert Sokolic

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13 February 2020

Christopher Choi

6

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13 February 2020

Elizabeth Garabedian

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13 February 2020

G Jayashree Jagadeesh

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13 February 2020

Pei-Yu Fu

11

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13 February 2020

Eric Gschweng

12

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13 February 2020

John F Tisdale

14

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13 February 2020

Kenneth I Weinberg

15

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13 February 2020

Neena Kapoor

17

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13 February 2020

Ami Shah

18

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13 February 2020

Hisham Abdel-Azim

19

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13 February 2020

Xiao-Jin Yu

20

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13 February 2020

Monika Smogorzewska

21

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13 February 2020

Alan S Wayne

22

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13 February 2020

Howard M Rosenblatt

23

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13 February 2020

Carla M Davis

24

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13 February 2020

Celine Hanson

25

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13 February 2020

Radha G Rishi

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13 February 2020

Xiaoyan Wang

27

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13 February 2020

David Gjertson

28

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13 February 2020

Otto O Yang

29

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13 February 2020

Arumugam Balamurugan

30

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13 February 2020

Gerhard Bauer

31

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13 February 2020

Joanna A Ireland

32

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13 February 2020

Barbara C Engel

33

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13 February 2020

Gregory M Podsakoff

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13 February 2020

Michael S Hershfield

35

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13 February 2020

R Michael Blaese

36

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13 February 2020

Robertson Parkman

37

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13 February 2020

language of work or name

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publication date

11 September 2012

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13 February 2020

1 reference

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13 February 2020

120

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13 February 2020

18

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13 February 2020

3635-3646

1 reference

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13 February 2020

Myeloid dysplasia and bone marrow hypocellularity in adenosine deaminase-deficient severe combined immune deficiency.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3488882

30 September 2017

Efficacy of gene therapy for X-linked severe combined immunodeficiency

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3488882

30 September 2017

Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease

1 reference

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30 September 2017

How I treat ADA deficiency

1 reference

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30 September 2017

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

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30 September 2017

Prolonged pancytopenia in a gene therapy patient with ADA-deficient SCID and trisomy 8 mosaicism: a case report

1 reference

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30 September 2017

Successful reconstitution of immunity in ADA-SCID by stem cell gene therapy following cessation of PEG-ADA and use of mild preconditioning

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3488882

30 September 2017

Long-term efficacy of enzyme replacement therapy for adenosine deaminase (ADA)-deficient severe combined immunodeficiency (SCID).

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3488882

30 September 2017

The many faces of IL-7: from lymphopoiesis to peripheral T cell maintenance

1 reference

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30 September 2017

Lymphocyte subsets in healthy children from birth through 18 years of age: the Pediatric AIDS Clinical Trials Group P1009 study

1 reference

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30 September 2017

The Moloney murine leukemia virus repressor binding site represses expression in murine and human hematopoietic stem cells

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30 September 2017

Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease

1 reference

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30 September 2017

Adenosine deaminase deficiency: genotype-phenotype correlations based on expressed activity of 29 mutant alleles

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30 September 2017

Consistent, persistent expression from modified retroviral vectors in murine hematopoietic stem cells

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30 September 2017

Development of improved adenosine deaminase retroviral vectors

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30 September 2017

Overview of biochemical abnormalities and molecular genetics of adenosine deaminase deficiency

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3488882

30 September 2017

Multiple modifications in cis elements of the long terminal repeat of retroviral vectors lead to increased expression and decreased DNA methylation in embryonic carcinoma cells.

1 reference

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30 September 2017

Effects of retroviral vector design on expression of human adenosine deaminase in murine bone marrow transplant recipients engrafted with genetically modified cells

1 reference

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30 September 2017

Engraftment of gene-modified umbilical cord blood cells in neonates with adenosine deaminase deficiency

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30 September 2017

Isolation of a recombinant murine leukemia virus utilizing a new primer tRNA.

1 reference

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30 September 2017

Embryonic stem cell virus, a recombinant murine retrovirus with expression in embryonic stem cells

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30 September 2017

Serum levels of IL-7 in bone marrow transplant recipients: relationship to clinical characteristics and lymphocyte count

1 reference

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28 June 2018

Transfer of the ADA gene into bone marrow cells and peripheral blood lymphocytes for the treatment of patients affected by ADA-deficient SCID.

1 reference

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28 June 2018

Antibody responses to bacteriophage phi X174 in patients with adenosine deaminase deficiency

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28 June 2018

Severe Combined Immunodeficiency and Adenosine Deaminase Deficiency

1 reference

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28 June 2018

Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction

1 reference

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21 September 2018

Long-term persistence of a polyclonal T cell repertoire after gene therapy for X-linked severe combined immunodeficiency

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3488882

21 September 2018

Gene therapy for immunodeficiency due to adenosine deaminase deficiency.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3488882

21 September 2018

Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3488882

21 September 2018

Treatment of adenosine deaminase deficiency with polyethylene glycol-modified adenosine deaminase

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3488882

21 September 2018

Adenosine-deaminase deficiency in two patients with severely impaired cellular immunity

1 reference

https://pubmed.ncbi.nlm.nih.gov/22968453

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Reference intervals for serum IgG, IgA, IgM, C3, and C4 as determined by rate nephelometry

1 reference

https://pubmed.ncbi.nlm.nih.gov/22968453

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Treatment of patients with severe combined immunodeficiency due to adenosine deaminase (ADA) deficiency by autologous transplantation of genetically modified bone marrow cells

1 reference

https://pubmed.ncbi.nlm.nih.gov/22968453

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Brief report: hepatic dysfunction as a complication of adenosine deaminase deficiency

1 reference

https://pubmed.ncbi.nlm.nih.gov/22968453

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Identifiers

10.1182/BLOOD-2012-02-400937

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13 February 2020

1 reference

Europe PubMed Central

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13 February 2020

1 reference

Europe PubMed Central

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13 February 2020

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