(Q45872713)

17 December 2017

title

Long-term persistence of a polyclonal T cell repertoire after gene therapy for X-linked severe combined immunodeficiency (English)

1 reference

17 December 2017

severe combined immunodeficiency

main subject

gene therapy

0 references

1 reference

Kimberly C Gilmour

3

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Adrian Thrasher

object named as

Adrian J Thrasher

12

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author name string

H Bobby Gaspar

1

1 reference

17 December 2017

Samantha Cooray

2

1 reference

17 December 2017

Kathryn L Parsley

4

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17 December 2017

Stuart Adams

5

1 reference

17 December 2017

Steven J Howe

6

1 reference

17 December 2017

Abdulaziz Al Ghonaium

7

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17 December 2017

Jinhua Bayford

8

1 reference

17 December 2017

Lucinda Brown

9

1 reference

17 December 2017

E Graham Davies

10

1 reference

17 December 2017

Christine Kinnon

11

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17 December 2017

language of work or name

English

0 references

publication date

1 August 2011

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17 December 2017

Science Translational Medicine

published in

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17 December 2017

volume

3

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17 December 2017

issue

97

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17 December 2017

page(s)

97ra79

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17 December 2017

Interleukin-2 receptor gamma chain mutation results in X-linked severe combined immunodeficiency in humans

cites work

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Severe combined immunodeficiency. A model disease for molecular immunology and therapy

21 January 2018

1 reference

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Cytokines and immunodeficiency diseases: critical roles of the gamma(c)-dependent cytokines interleukins 2, 4, 7, 9, 15, and 21, and their signaling pathways

21 January 2018

1 reference

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Hematopoietic stem-cell transplantation for the treatment of severe combined immunodeficiency.

21 January 2018

1 reference

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Transplantation of hematopoietic stem cells and long-term survival for primary immunodeficiencies in Europe: entering a new century, do we do better?

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Failure of SCID-X1 gene therapy in older patients

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Long-term outcome after hematopoietic stem cell transplantation of a single-center cohort of 90 patients with severe combined immunodeficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Severe cutaneous papillomavirus disease after haemopoietic stem-cell transplantation in patients with severe combined immune deficiency caused by common gammac cytokine receptor subunit or JAK-3 deficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Efficacy of gene therapy for X-linked severe combined immunodeficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Self-inactivating gammaretroviral vectors for gene therapy of X-linked severe combined immunodeficiency.

21 January 2018

1 reference

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A self-inactivating lentiviral vector for SCID-X1 gene therapy that does not activate LMO2 expression in human T cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Gene therapy for immunodeficiency due to adenosine deaminase deficiency.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Successful reconstitution of immunity in ADA-SCID by stem cell gene therapy following cessation of PEG-ADA and use of mild preconditioning

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

SpA: web-accessible spectratype analysis: data management, statistical analysis and visualization

21 January 2018

1 reference

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High-throughput multiplexed T-cell-receptor excision circle quantitative PCR assay with internal controls for detection of severe combined immunodeficiency in population-based newborn screening.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Lentiviral vectors containing an enhancer-less ubiquitously acting chromatin opening element (UCOE) provide highly reproducible and stable transgene expression in hematopoietic cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCITRANSLMED.3002715

Long-term survival and transplantation of haemopoietic stem cells for immunodeficiencies: report of the European experience 1968–99

21 January 2018

1 reference

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Changes in thymic function with age and during the treatment of HIV infection

21 January 2018

1 reference

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10.1126/SCITRANSLMED.3002715

21 January 2018

Identifiers

DOI

1 reference

17 December 2017

PubMed ID

21865537

1 reference

17 December 2017