(Q37295134)

English

A novel human gamma-globin gene vector for genetic correction of sickle cell anemia in a humanized sickle mouse model: critical determinants for successful correction

scientific article published on 27 May 2009

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scholarly article

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

A novel human gamma-globin gene vector for genetic correction of sickle cell anemia in a humanized sickle mouse model: critical determinants for successful correction (English)

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

sickle-cell disease

0 references

author name string

Ajay Perumbeti

1

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

Tomoyasu Higashimoto

2

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

Fabrizia Urbinati

3

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

Robert Franco

4

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

Herbert J Meiselman

5

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

David Witte

6

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

Punam Malik

7

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

language of work or name

0 references

publication date

27 May 2009

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

114

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

6

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

1174-1185

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

Correction of murine sickle cell disease using gamma-globin lentiviral vectors to mediate high-level expression of fetal hemoglobin

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

An experimental system for the evaluation of retroviral vector design to diminish the risk for proto-oncogene activation

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

Pathology of Berkeley sickle cell mice: similarities and differences with human sickle cell disease

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

Hematopoietic stem cell transplantation for multiply transfused patients with sickle cell disease and thalassemia after low-dose total body irradiation, fludarabine, and rabbit anti-thymocyte globulin

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

Blood rheology and hemodynamics

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

Effect of hydroxyurea on mortality and morbidity in adult sickle cell anemia: risks and benefits up to 9 years of treatment

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

Correction of sickle cell disease in transgenic mouse models by gene therapy

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

T lymphocytes with a normal ADA gene accumulate after transplantation of transduced autologous umbilical cord blood CD34+ cells in ADA-deficient SCID neonates.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

Time-dependent changes in the density and hemoglobin F content of biotin-labeled sickle cells

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

Barriers to bone marrow transplantation for sickle cell anemia.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

6 September 2017

Lenti in red: progress in gene therapy for human hemoglobinopathies

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

14 September 2017

A cure for murine sickle cell disease through stable mixed chimerism and tolerance induction after nonmyeloablative conditioning and major histocompatibility complex-mismatched bone marrow transplantation

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

14 September 2017

A chromatin insulator blocks interactions between globin regulatory elements and cellular promoters in erythroid cells

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

26 June 2018

Second generation knockout sickle mice: the effect of HbF.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

26 June 2018

Hydroxyurea-induced augmentation of fetal hemoglobin production in patients with sickle cell anemia.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

26 June 2018

Gene therapy for immunodeficiency due to adenosine deaminase deficiency.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Stable long-term donor engraftment following reduced-intensity hematopoietic cell transplantation for sickle cell disease

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Late effects of myeloablative bone marrow transplantation (BMT) in sickle cell disease (SCD).

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Improved human beta-globin expression from self-inactivating lentiviral vectors carrying the chicken hypersensitive site-4 (cHS4) insulator element

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Circumstances of death in adult sickle cell disease patients.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

A genetic strategy to treat sickle cell anemia by coregulating globin transgene expression and RNA interference

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Successful correction of the human beta-thalassemia major phenotype using a lentiviral vector

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Chimerism and cure: hematologic and pathologic correction of murine sickle cell disease.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Correction of a mouse model of sickle cell disease: lentiviral/antisickling beta-globin gene transduction of unmobilized, purified hematopoietic stem cells

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Results of minimally toxic nonmyeloablative transplantation in patients with sickle cell anemia and beta-thalassemia

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Transduced CD34+ cells from adrenoleukodystrophy patients with HIV-derived vector mediate long-term engraftment of NOD/SCID mice.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

The degree of phenotypic correction of murine beta -thalassemia intermedia following lentiviral-mediated transfer of a human gamma-globin gene is influenced by chromosomal position effects and vector copy number

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Stable mixed hematopoietic chimerism after bone marrow transplantation for sickle cell anemia.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

High-level erythroid-specific gene expression in primary human and murine hematopoietic cells with self-inactivating lentiviral vectors

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Locus control region activity by 5'HS3 requires a functional interaction with beta-globin gene regulatory elements: expression of novel beta/gamma-globin hybrid transgenes

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Clinical potential of in vitro measured red cell deformability, a myth?

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Genetic correction of sickle cell disease: insights using transgenic mouse models

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Fetal hemoglobin and F-cell responses to long-term hydroxyurea treatment in young sickle cell patients. The French Study Group on Sickle Cell Disease.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Transgenic knockout mice with exclusively human sickle hemoglobin and sickle cell disease

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Mortality in sickle cell disease. Life expectancy and risk factors for early death.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 September 2018

Long-term results of related myeloablative stem-cell transplantation to cure sickle cell disease

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2723013

3 December 2018

Variation in fetal hemoglobin parameters and predicted hemoglobin S polymerization in sickle cell children in the first two years of life: Parisian Prospective Study on Sickle Cell Disease

1 reference

https://pubmed.ncbi.nlm.nih.gov/19474450

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

2-deoxy 5-azacytidine and fetal hemoglobin induction in sickle cell anemia

1 reference

https://pubmed.ncbi.nlm.nih.gov/19474450

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Bone marrow transplantation without myeloablation for sickle cell disease

1 reference

https://pubmed.ncbi.nlm.nih.gov/19474450

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Effects of mixed hematopoietic chimerism in a mouse model of bone marrow transplantation for sickle cell anemia

1 reference

https://pubmed.ncbi.nlm.nih.gov/19474450

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Sickle cell disease of transgenic SAD mice

1 reference

https://pubmed.ncbi.nlm.nih.gov/19474450

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Hemoglobin-specific antibody in a multiply transfused patient with sickle cell disease

1 reference

https://pubmed.ncbi.nlm.nih.gov/19474450

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

National trends in the mortality of children with sickle cell disease, 1968 through 1992

1 reference

https://pubmed.ncbi.nlm.nih.gov/19474450

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Physiologic decline in fetal hemoglobin parameters in infants with sickle cell disease: implications for pharmacological intervention

1 reference

https://pubmed.ncbi.nlm.nih.gov/19474450

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Identifiers

10.1182/BLOOD-2009-01-201863

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

PMC publication ID

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

PubMed publication ID

1 reference

Europe PubMed Central

PMC publication ID

19 August 2017

ResearchGate publication ID

0 references

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