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English
An analysis of retinal gene therapy clinical trials.
scientific article published on October 2009
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scholarly article
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
review article
1 reference
stated in
Europe PubMed Central
title
An analysis of retinal gene therapy clinical trials
(English)
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
main subject
gene therapy
0 references
author name string
Robert E MacLaren
series ordinal
1
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
publication date
1 October 2009
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
published in
Current Opinion in Molecular Therapeutics
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
volume
11
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
issue
5
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
page(s)
540-546
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
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Safety of recombinant adeno-associated virus type 2-RPE65 vector delivered by ocular subretinal injection
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1 September 2018
Adenoviral vector-delivered pigment epithelium-derived factor for neovascular age-related macular degeneration: results of a phase I clinical trial
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1 September 2018
Gene therapy restores vision-dependent behavior as well as retinal structure and function in a mouse model of RPE65 Leber congenital amaurosis
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PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2896974
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1 September 2018
Cone opsin mislocalization in Rpe65-/- mice: a defect that can be corrected by 11-cis retinal
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reference URL
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1 September 2018
11-cis-retinal reduces constitutive opsin phosphorylation and improves quantum catch in retinoid-deficient mouse rod photoreceptors
1 reference
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PubMed Central
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1 September 2018
Identification of the RPE65 protein in mammalian cone photoreceptors.
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1 September 2018
In vivo gene transfer to the mouse eye using an HIV-based lentiviral vector; efficient long-term transduction of corneal endothelium and retinal pigment epithelium
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1 September 2018
Effect of Rpe65 knockout on accumulation of lipofuscin fluorophores in the retinal pigment epithelium.
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PubMed Central
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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2896974
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1 September 2018
Gene therapy restores vision in a canine model of childhood blindness
1 reference
stated in
PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2896974
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1 September 2018
CMV-beta-actin promoter directs higher expression from an adeno-associated viral vector in the liver than the cytomegalovirus or elongation factor 1 alpha promoter and results in therapeutic levels of human factor X in mice
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PubMed Central
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1 September 2018
Gene transfer into the mouse retina mediated by an adeno-associated viral vector
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PubMed Central
reference URL
https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2896974
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1 September 2018
Role of the 3'-untranslated region of RPE65 mRNA in the translational regulation of the RPE65 gene: identification of a specific translation inhibitory element
1 reference
stated in
PubMed
reference URL
https://pubmed.ncbi.nlm.nih.gov/19806502
retrieved
12 December 2020
based on heuristic
inferred from PubMed ID database lookup
AAV vectors, insertional mutagenesis, and cancer
1 reference
stated in
PubMed
reference URL
https://pubmed.ncbi.nlm.nih.gov/19806502
retrieved
12 December 2020
based on heuristic
inferred from PubMed ID database lookup
Identifiers
PMC publication ID
2896974
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
PubMed publication ID
19806502
1 reference
stated in
Europe PubMed Central
PMC publication ID
2896974
reference URL
https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19806502%20AND%20SRC:MED&resulttype=core&format=json
retrieved
9 February 2020
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