(Q37974988)

26 August 2017

title

Homologous recombination-based gene therapy for the primary immunodeficiencies (English)

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26 August 2017

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Matthew Porteus

1

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26 August 2017

language of work or name

English

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publication date

1 December 2011

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Annals of the New York Academy of Sciences

26 August 2017

published in

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26 August 2017

volume

1246

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26 August 2017

page(s)

131-140

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Advances in the understanding and treatment of human severe combined immunodeficiency

26 August 2017

cites work

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Gene therapy for severe combined immunodeficiency

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Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.

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Chimeric nucleases stimulate gene targeting in human cells

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Targeted mutation of the Hprt gene in mouse embryonic stem cells

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Insertion of DNA sequences into the human chromosomal beta-globin locus by homologous recombination

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Clarifying the mechanics of DNA strand exchange in meiotic recombination

21 January 2018

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Hybrid restriction enzymes: zinc finger fusions to Fok I cleavage domain

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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A simple cipher governs DNA recognition by TAL effectors

21 January 2018

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21 January 2018

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Gene therapy for primary immunodeficiencies: looking ahead, toward gene correction

21 January 2018

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21 January 2018

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Gene targeting of a disease-related gene in human induced pluripotent stem and embryonic stem cells

21 January 2018

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21 January 2018

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Genetic engineering of human pluripotent cells using TALE nucleases

21 January 2018

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10.1111/J.1749-6632.2011.06314.X

21 January 2018

Identifiers

DOI

1 reference

26 August 2017

1 reference