(Q40140649)

17 September 2017

title

A New AAV10-U7-Mediated Gene Therapy Prolongs Survival and Restores Function in an ALS Mouse Model (English)

1 reference

amyotrophic lateral sclerosis

17 September 2017

0 references

1 reference

Maria Grazia Biferi

1

1 reference

17 September 2017

Mathilde Cohen-Tannoudji

2

1 reference

17 September 2017

Ambra Cappelletto

3

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17 September 2017

Benoit Giroux

4

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17 September 2017

Marianne Roda

5

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17 September 2017

Stéphanie Astord

6

1 reference

17 September 2017

Thibaut Marais

7

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17 September 2017

Corinne Bos

8

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17 September 2017

Thomas Voit

9

1 reference

17 September 2017

Arnaud Ferry

10

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17 September 2017

Martine Barkats

11

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17 September 2017

publication date

26 June 2017

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17 September 2017

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17 September 2017

volume

25

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17 September 2017

issue

9

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17 September 2017

page(s)

2038-2052

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describes a project that uses

17 September 2017

ImageJ

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC5589057/fullTextXML

based on heuristic

inferred from PubMed Central ID database lookup

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

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30 August 2018

1 reference

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Lentiviral-mediated silencing of SOD1 through RNA interference retards disease onset and progression in a mouse model of ALS.

30 August 2018

1 reference

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Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping

30 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5589057

The special Sm core structure of the U7 snRNP: far-reaching significance of a small nuclear ribonucleoprotein

30 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5589057

2'-O-methyl-modified phosphorothioate antisense oligonucleotides have reduced non-specific effects in vitro

30 August 2018

1 reference

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30 August 2018

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Listening to silence and understanding nonsense: exonic mutations that affect splicing

30 August 2018

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5589057

Myosin heavy chain isoform expression following reduced neuromuscular activity: potential regulatory mechanisms

30 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5589057

A rule for termination-codon position within intron-containing genes: when nonsense affects RNA abundance

30 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5589057

Motor neurons in Cu/Zn superoxide dismutase-deficient mice develop normally but exhibit enhanced cell death after axonal injury

30 August 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5589057

Mutations in Cu/Zn superoxide dismutase gene are associated with familial amyotrophic lateral sclerosis

30 August 2018

1 reference

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A controlled trial of riluzole in amyotrophic lateral sclerosis. ALS/Riluzole Study Group

30 August 2018

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2017.05.017

Skeletal Muscle Is a Primary Target of SOD1G93A-Mediated Toxicity

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2017.05.017

Exosome-associated AAV vector as a robust and convenient neuroscience tool

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2017.05.017

Selective silencing of mutated mRNAs in DM1 by using modified hU7-snRNAs

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2017.05.017

Transgenic-mouse model of amyotrophic lateral sclerosis

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2017.05.017

10.1016/J.YMTHE.2017.05.017

7 January 2021

Identifiers

DOI

1 reference

17 September 2017

0 references

1 reference